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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Gene Therapy Trial for Otoferlin Gene-mediated Hearing LossDeafness, Deafness, Autosomal Recessive 9, Ear Diseases, Hearing Loss, Bilateral, Hearing Loss, Sensorineural, Neurologic Manifestations, Pathological Conditions, Signs and Symptoms, Sensation Disorders, Signs and Symptoms, auditory neuropathy, hearing disorder, hearing loss disorder, nervous system disorder, otorhinolaryngologic diseaseRecruitingPhase 32026-09-29NCT05821959
Otoferlin Gene-mediated Hearing Loss Natural History StudyEar Diseases, Hearing Loss, Sensorineural, Neurologic Manifestations, Pathological Conditions, Signs and Symptoms, Sensation Disorders, Signs and Symptoms, auditory neuropathy, hearing disorder, hearing loss disorder, nervous system disorder, otorhinolaryngologic diseaseRecruitingNot stated2026-03-04NCT05572073