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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
A Prospective Registry Study to Assess Real-world Patient Characteristics, Treatment Patterns, and Longitudinal Outcomes in Patients Receiving Mavacamten and Other Treatments for Symptomatic Obstructive Hypertrophic Cardiomyopathy (Obstructive-HCM)aortic valve disorder, aortic valve stenosis, cardiomyopathy, cardiovascular disorder, heart disorder, heart failure, heart valve disorder, hypertrophic cardiomyopathy, subvalvular aortic stenosisRecruitingNot stated2026-08-19NCT05489705
MEASuRE: Metreleptin Effectiveness And Safety RegistryCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Lipid Metabolism Disorders, Lipid Metabolism, Inborn Errors, Nutritional and Metabolic Diseases, Skin Diseases, Metabolic, Skin and Connective Tissue Diseases, acquired partial lipodystrophy, congenital generalized lipodystrophy, hereditary disease, inborn errors of metabolism, lipodystrophy, metabolic disease, partial lipodystrophy, skin disorderRecruitingNot stated2026-07-16NCT02325674
A Study of TAK-330 to Reverse the Effects of Factor Xa Inhibitors For Adults Needing Urgent SurgeryHemic and Lymphatic Diseases, blood coagulation disease, cardiovascular disorder, hematologic disorder, hemorrhagic disease, vascular disorder, vascular hemostatic diseaseRecruitingPhase 32026-06-18NCT05156983
Intraamniotic Administrations of ER004 to Male Subjects With X-linked Hypohidrotic Ectodermal DysplasiaAbnormalities, Multiple, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Ectodermal Dysplasia 1, Anhidrotic, Skin Abnormalities, Skin and Connective Tissue Diseases, X-linked disease, ectodermal dysplasia syndrome, hereditary disease, hereditary skin disorder, skin disorderRecruitingPhase 22025-04-30NCT04980638