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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
A Long-term Follow-up Study Evaluating Intravenous Injection of EXG001-307 in Patients With Type 1 SMAcentral nervous system disorder, motor neuron disorder, nervous system disorder, neurodegenerative disease, neuromuscular disease, spinal cord disorder, spinal muscular atrophyEnrolling by invitationNot stated2025-03-05NCT06588803