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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
EncompaSSc: Evaluation of MTX-474 in Participants With Diffuse Cutaneous Systemic Sclerosis (dcSSc)Skin and Connective Tissue Diseases, connective tissue disorder, diffuse scleroderma, skin disorder, systemic sclerosisRecruitingPhase 22026-10-05NCT07287670
A Study to Compare Elritercept to Placebo in Adults With Myelofibrosis and Anemia Who Are Taking RuxolitinibHemic and Lymphatic Diseases, Myeloproliferative Disorders, anemia, bone marrow disorder, hematologic disorder, primary myelofibrosisRecruitingPhase 32026-10-01NCT07623161
Parasitic Ulcer Treatment TrialAcanthamoeba keratitis, Infections, amebiasis, corneal disorder, corneal ulcer, eye disorder, eye infectious disorder, keratitis, parasitic eye infection, parasitic infectious disease, protozoa infectious diseaseRecruitingPhase 32026-10-01NCT06213649
Nectero EAST System Clinical StudyAneurysm, abdominal aortic aneurysm, aortic aneurysm, aortic disorder, cardiovascular disorder, vascular disorderRecruitingPhase 2 / Phase 32026-09-28NCT06001918
Platform Clinical Study for Conquering SclerodermaSkin and Connective Tissue Diseases, connective tissue disorder, diffuse scleroderma, interstitial lung disease, lung disorder, respiratory system disorder, scleroderma, skin disorder, systemic sclerosisRecruitingPhase 22026-08-18NCT06195072
Pioglitazone Versus Empagliflozin for Chronic Pancreatitis/Recurrent Acute Pancreatitis/Acute Pancreatitis Associated Diabetes MellitusChronic Disease, Digestive System Diseases, Disease Attributes, Nutritional and Metabolic Diseases, Pathologic Processes, Pathological Conditions, Signs and Symptoms, acute pancreatitis, chronic pancreatitis, diabetes mellitus, endocrine system disorder, glucose metabolism disease, metabolic disease, pancreas disorder, pancreatitisRecruitingPhase 22026-07-29NCT06729996
Assessment of Combined CCM and ICD Device in HFrEFArrhythmias, Cardiac, Cardiac Conduction System Disease, Death, Death, Sudden, Death, Sudden, Cardiac, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Tachycardia, cardiac arrest, cardiovascular disorder, heart disorder, heart failure, sudden cardiac arrest, ventricular fibrillation, ventricular tachycardiaActive, not recruitingNot applicable2026-05-27NCT05855135
MAGNITUDE: A Phase 3 Study of NTLA-2001 in Participants With Transthyretin Amyloidosis With Cardiomyopathy (ATTR-CM)Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Nutritional and Metabolic Diseases, amyloidosis, cardiomyopathy, cardiovascular disorder, familial amyloid neuropathy, heart disorder, hereditary amyloidosis, hereditary disease, inborn errors of metabolism, metabolic disease, proteostasis deficienciesRecruitingPhase 32026-03-27NCT06128629
Colorectal Cancer Screening in Cystic FibrosisCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, Digestive System Neoplasms, Infant, Newborn, Diseases, Neoplasms by Histologic Type, Neoplasms by Site, adenoma, colonic disorder, colorectal cancer, colorectal neoplasm, cystic fibrosis, digestive system disorder, digestive system neoplasm, epithelial neoplasm, hereditary disease, intestinal disorder, lung disorder, neoplasm, pancreas disorder, rectal disorder, respiratory system disorderActive, not recruitingNot stated2026-03-24NCT05362344
Phase III Trial of Anlotinib, Catequentinib in Advanced Alveolar Soft Part Sarcoma, Leiomyosarcoma, Synovial Sarcoma (APROMISS)Neoplasms by Histologic Type, Neoplasms, Connective and Soft Tissue, alveolar soft part sarcoma, connective tissue neoplasm, leiomyosarcoma, myomatous neoplasm, neoplasm, sarcoma, synovial sarcomaRecruitingPhase 32026-02-25NCT03016819
Evaluation of Symphony™ Posterior Cervical System for Surgical Treatment of Adult Cervical DeformityKyphosis, Spinal Curvatures, bone disorder, musculoskeletal system disorder, scoliosis, vertebral column disorderActive, not recruitingNot stated2026-02-17NCT04912674
Radiographic and Clinical Evaluation of Surgical Treatment for Cervical Deformity: A Multi-Center Study 2.0Kyphosis, Spinal Curvatures, bone disorder, musculoskeletal system disorder, scoliosis, vertebral column disorderRecruitingNot stated2026-02-17NCT04194996
The Myelin Disorders Biorepository ProjectAbnormalities, Multiple, Aicardi-Goutieres syndrome, Alexander disease, Alexanders leukodystrophy, Allan-Herndon-Dudley syndrome, Bone Diseases, Developmental, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Canavan disease, Cerebral Small Vessel Diseases, Charcot-Marie-Tooth disease, Cockayne syndrome, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, DNA repair disease, Digestive System Diseases, Dwarfism, Female Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, GM2 gangliosidosis, Gangliosidoses, Hereditary Central Nervous System Demyelinating Diseases, Infant, Newborn, Diseases, Infarction, Krabbe disease, Leukoencephalopathies, Lipid Metabolism Disorders, Lipid Metabolism, Inborn Errors, Lysosomal Storage Diseases, Nervous System, Male Urogenital Diseases, Necrosis, Neurobehavioral Manifestations, Neurologic Manifestations, Nutritional and Metabolic Diseases, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Pelizaeus-Merzbacher spectrum disorder, Peroxisomal Disorders, Salla disease, Sjogren syndrome, Sjogren-Larsson syndrome, Skin Abnormalities, Skin and Connective Tissue Diseases, Stomatognathic Diseases, Sulfatidosis, Urogenital Diseases, X-linked disease, Xerostomia, Zellweger spectrum disorders, adrenal gland disorder, adrenocortical insufficiency, adrenoleukodystrophy, adrenomyeloneuropathy, adult Refsum disease, adult-onset autosomal dominant demyelinating leukodystrophy, alpha-gal syndrome, arthritic joint disease, arthropathy, attention deficit hyperactivity disorder, inattentive type, autoimmune disease, bone disorder, brain disorder, brain infarction, brain ischemia, cardiovascular disorder, central nervous system disorder, central nervous system malformation, cerebral arterial disease, cerebral infarction, cerebrotendinous xanthomatosis, cerebrovascular disorder, connective tissue disorder, cutaneous mucinosis, dementia, demyelinating disease, dry eye syndrome, endocrine system disorder, eye disorder, hereditary disease, hereditary motor and sensory neuropathy, hereditary skin disorder, hypomyelination with brain stem and spinal cord involvement and leg spasticity, ichthyosis, immune system disorder, inborn carbohydrate metabolic disorder, inborn errors of metabolism, inherited neurodegenerative disorder, intellectual disability, intracranial arterial disease, ischemic disease, keratosis, kidney disorder, lacrimal apparatus disorder, leukodystrophy, leukodystrophy, hypomyelinating, 5, leukodystrophy, hypomyelinating, 6, leukodystrophy, hypomyelinating, 7, with or without oligodontia and/or hypogonadotropic hypogonadism, leukoencephalopathy with brain stem and spinal cord involvement-high lactate syndrome, leukoencephalopathy with calcifications and cysts, leukoencephalopathy with vanishing white matter 1, leukoencephalopathy, diffuse hereditary, with spheroids 1, liver disorder, lysosomal lipid storage disorder, lysosomal storage disease, megalencephalic leukoencephalopathy with subcortical cysts, metabolic disease, metachromatic leukodystrophy, mouth disorder, mucopolysaccharidosis, mucosulfatidosis, musculoskeletal system disorder, nervous system disorder, neurodegeneration with brain iron accumulation 5, neurodegenerative disease, neurodevelopmental disorder, neuromuscular disease, null syndrome, oppositional defiant disorder, peripheral nervous system disorder, polyneuropathy, psychiatric disorder, rheumatic disorder, rheumatoid arthritis, salivary gland disorder, skin disorder, sphingolipidosis, stroke disorder, urinary system disorder, vascular dementia, vascular disorder, xanthomatosisRecruitingNot stated2025-10-23NCT03047369
Prospective Data Registry and Quality of Life Assessment of Patients Undergoing Radiotherapy With the RefleXion Medical Radiotherapy SystemCancer of Gastrointestinal Tract, Digestive System Diseases, Digestive System Neoplasms, Female Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Genitourinary Cancer, Head and Neck Neoplasms, Male Urogenital Diseases, Neoplasms by Site, Urogenital Diseases, Urogenital Neoplasms, cancer, central nervous system cancer, digestive system disorder, digestive system neoplasm, neoplasm, nervous system disorderRecruitingNot stated2025-08-15NCT05406167
International Rare Histiocytic Disorders Registry (IRHDR)Collagen Diseases, Erdheim-Chester disease, Granuloma, Hemic and Lymphatic Diseases, Lipid Metabolism Disorders, Necrobiotic Disorders, Nutritional and Metabolic Diseases, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Skin and Connective Tissue Diseases, connective tissue disorder, histiocytosis, lymphatic system disorder, lymphoproliferative syndrome, metabolic disease, necrobiotic xanthogranuloma, non-Langerhans cell histiocytosis, sinus histiocytosis with massive lymphadenopathy, skin disorder, xanthomatosisRecruitingNot stated2025-06-24NCT02285582
The OPBC-07/microNAC StudyNeoplasms by Site, Skin and Connective Tissue Diseases, breast cancer, breast disorder, breast neoplasm, neoplasm, skin disorderActive, not recruitingNot stated2025-01-24NCT06529302