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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
An Open Label Individual Patient (OLIP)-02 Study of Nusinersen (BIIB058)central nervous system disorder, motor neuron disorder, nervous system disorder, neurodegenerative disease, neuromuscular disease, spinal cord disorder, spinal muscular atrophyNot yet recruitingPhase 32026-09-29NCT07846696
An OLIP Study (Open Label Individual Patient) of Nusinersen in a Participant With Spinal Muscular Atrophy Who Previously Participated in an Investigational Study With Nusinersencentral nervous system disorder, motor neuron disorder, nervous system disorder, neurodegenerative disease, neuromuscular disease, spinal cord disorder, spinal muscular atrophyNot yet recruitingNot applicable2026-09-24NCT07838779
Advancing Brain Outcomes in Pediatric Critically Ill Patients Sedated With Volatile AnEsthestic AgentsPathologic Processes, Pathological Conditions, Signs and Symptoms, Respiration Disorders, Respiratory Aspiration, respiratory system disorderRecruitingPhase 32026-02-04NCT05867472
Extension Study of Infigratinib in Children With Achondroplasia (ACH)Bone Diseases, Developmental, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Dwarfism, Nutritional and Metabolic Diseases, Skin and Connective Tissue Diseases, achondroplasia, bone disorder, connective tissue disorder, cutaneous mucinosis, hereditary disease, inborn carbohydrate metabolic disorder, inborn errors of metabolism, lysosomal storage disease, metabolic disease, mucopolysaccharidosis, mucopolysaccharidosis type 4, musculoskeletal system disorder, osteochondrodysplasiaEnrolling by invitationPhase 22025-10-31NCT05145010
POHCA Resuscitation: Evaluation of IM Epinephrinecardiac arrest, cardiovascular disorder, heart disorderRecruitingPhase 2 / Phase 32025-03-11NCT05166343