Boston Childrens Hospital
Boston Childrens Hospital
Boston, Massachusetts, United States15 results · Page 1 of 1
Clinical trials
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| Trial | Conditions | Status | Phase | Updated | More info | NCT ID |
|---|---|---|---|---|---|---|
| Pharmacokinetics, Safety, and Efficacy of Povorcitinib in Adolescent Participants With Moderate to Severe Hidradenitis Suppurativa | Bacterial Infections and Mycoses, Infections, Skin and Connective Tissue Diseases, Suppuration, bacterial infectious disease, hidradenitis, hidradenitis suppurativa, skin disease caused by bacterial infection, skin disorder, skin disorder caused by infection, sweat gland disorder | Recruiting | Phase 2 | 2026-10-09 | NCT07213973 | |
| A Study of Guselkumab in Pediatric Participants With Moderately to Severely Active Crohn's Disease | Crohn disease, Digestive System Diseases, digestive system disorder, gastroenteritis, inflammatory bowel disease, intestinal disorder | Recruiting | Phase 3 | 2026-09-25 | NCT05923073 | |
| A Study of Nipocalimab in Pregnancies at Risk for Severe Hemolytic Disease of the Fetus and Newborn (HDFN) | Hemolytic Disease of the Fetus and Newborn | Recruiting | Phase 3 | 2026-09-25 | NCT05912517 | |
| A Study of Ocrelizumab in Children and Adolescents With Relapsing-Remitting Multiple Sclerosis | CNS demyelinating autoimmune disease, autoimmune disease, autoimmune disorder of the nervous system, demyelinating disease, immune system disorder, multiple sclerosis, nervous system disorder | Active, not recruiting | Phase 2 | 2026-09-14 | NCT04075266 | |
| A Study to Investigate the Safety and Efficacy of RO7204239 in Combination With Risdiplam (RO7034067) in Participants With Spinal Muscular Atrophy | central nervous system disorder, motor neuron disorder, nervous system disorder, neurodegenerative disease, neuromuscular disease, spinal cord disorder, spinal muscular atrophy | Active, not recruiting | Phase 2 / Phase 3 | 2026-09-09 | NCT05115110 | |
| A U.S. Registry of Eosinophilic Esophagitis Pediatric, Adolescent and Adult Patients Treated With DUPIXENT® As Standard of Care | Digestive System Diseases, Eosinophilia, Hemic and Lymphatic Diseases, Hypersensitivity, Immediate, digestive system disorder, eosinophilic esophagitis, esophageal disorder, esophagitis, gastroenteritis, hematologic disorder, immune system disorder, leukocyte disorder | Active, not recruiting | Not stated | 2026-08-12 | NCT06693531 | |
| Nucleoside Therapy in Patients With Telomere Biology Disorders | Bone Marrow Failure Disorders, Congenital Abnormalities, Congenital Bone Marrow Failure Syndromes, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Fibrosis, Hemic and Lymphatic Diseases, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Revesz syndrome, Skin Abnormalities, Skin and Connective Tissue Diseases, X-linked disease, bone marrow disorder, dyskeratosis congenita, hematologic disorder, hereditary disease, hereditary skin disorder, interstitial lung disease, lung disorder, pulmonary fibrosis, respiratory system disorder, skin disorder | Recruiting | Phase 1 | 2026-08-04 | NCT06817590 | |
| A Study to Evaluate Long-term Safety of Ecopipam Tablets in Children, Adolescents and Adults With Tourette's Disorder | Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Tourette syndrome, basal ganglia disorder, brain disorder, central nervous system disorder, hereditary disease, inherited neurodegenerative disorder, movement disorder, nervous system disorder, neurodegenerative disease, neurodevelopmental disorder, psychiatric disorder, tic disorder | Active, not recruiting | Phase 3 | 2026-07-22 | NCT06021522 | |
| guideSEQ: Genomic Understanding, Impact, Decision & Ethics in Prenatal Sequencing | Prenatal Genetic Diagnosis | Recruiting | Not applicable | 2026-07-15 | NCT07610590 | |
| Study to Evaluate Efficacy and Safety of Romosozumab Compared With Bisphosphonates in Children and Adolescents With Osteogenesis Imperfecta | Bone Diseases, Developmental, Collagen Diseases, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Skin and Connective Tissue Diseases, bone disorder, connective tissue disorder, hereditary disease, musculoskeletal system disorder, osteochondrodysplasia, osteogenesis imperfecta | Active, not recruiting | Phase 3 | 2026-05-27 | NCT05972551 | |
| Registry and Natural History Study for Progressive Myoclonus Epilepsy Type 1 (EPM1) | Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Dyskinesias, Epilepsies, Myoclonic, Epilepsy, Generalized, Epileptic Syndromes, Myoclonus, Neurologic Manifestations, Pathological Conditions, Signs and Symptoms, Signs and Symptoms, Unverricht-Lundborg syndrome, brain disorder, central nervous system disorder, epilepsy, hereditary disease, inherited neurodegenerative disorder, nervous system disorder, neurodegenerative disease, progressive myoclonus epilepsy | Recruiting | Not stated | 2026-03-18 | NCT06593951 | |
| Phase I/II Trial of Lentiviral Gene Transfer for SCID-X1 With Low Dose Targeted Busulfan Conditioning | Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Infant, Newborn, Diseases, Primary Immunodeficiency Diseases, X-Linked Combined Immunodeficiency Diseases, X-linked disease, hereditary disease, immune system disorder, inborn error of immunity, severe combined immunodeficiency | Recruiting | Phase 1 / Phase 2 | 2025-12-11 | NCT03311503 | |
| Mycobacteriophage Treatment of Non-tuberculosis Mycobacteria | Actinomycetales infectious disease, Bacterial Infections and Mycoses, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, Infant, Newborn, Diseases, Infections, Mycobacterium Infections, Nontuberculous, bacterial infectious disease, cystic fibrosis, gram-positive bacterial infections, hereditary disease, lung disorder, mycobacterial infectious disease, pancreas disorder, pulmonary non-tuberculous mycobacterial infection, respiratory system disorder | Enrolling by invitation | Not stated | 2025-05-21 | NCT06262282 | |
| Effects of Ketosis on Brain Function in Patients With T1DM | Acid-Base Imbalance, Ketosis, Nutritional and Metabolic Diseases, acidosis disorder, metabolic disease | Recruiting | Not applicable | 2024-12-18 | NCT04219709 | |
| MASA Valve Early Feasibility Study | Cardiovascular Abnormalities, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Pulmonary Atresia, Ventricular Outflow Obstruction, aortopulmonary window, cardiovascular disorder, congenital heart disease, heart disorder, heart septal defect, heart valve disorder, persistent truncus arteriosus, pulmonary valve stenosis, pulmonic stenosis, tetralogy of fallot, transposition of the great arteries, vascular malformation | Recruiting | Not applicable | 2024-11-06 | NCT05452720 |