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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
LGMD R1 Natural History StudyCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Muscular Disorders, Atrophic, autosomal recessive limb-girdle muscular dystrophy type 2A, hereditary disease, limb-girdle muscular dystrophy, muscle tissue disorder, muscular dystrophy, musculoskeletal system disorder, nervous system disorder, neuromuscular diseaseActive, not recruitingNot stated2026-06-10NCT05618080