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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Pridopidine Phase 3 Study in Huntington's DiseaseCognition Disorders, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Dyskinesias, Huntington disease, basal ganglia disorder, brain disorder, central nervous system disorder, choreatic disease, cognitive disorder, dementia, hereditary disease, inherited neurodegenerative disorder, movement disorder, nervous system disorder, neurodegenerative disease, psychiatric disorderRecruitingPhase 32026-10-07NCT07609108
A Study to Investigate Mibavademab in Adult Women With Functional Hypothalamic AmenorrheaFemale Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Genital Diseases, Menstruation Disturbances, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Urogenital Diseases, amenorrhea, female infertility, female reproductive system disorder, functional hypothalamic amenorrhea, infertility disorderRecruitingPhase 22026-10-01NCT07235917
MAGNITUDE: A Phase 3 Study of NTLA-2001 in Participants With Transthyretin Amyloidosis With Cardiomyopathy (ATTR-CM)Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Nutritional and Metabolic Diseases, amyloidosis, cardiomyopathy, cardiovascular disorder, familial amyloid neuropathy, heart disorder, hereditary amyloidosis, hereditary disease, inborn errors of metabolism, metabolic disease, proteostasis deficienciesRecruitingPhase 32026-03-27NCT06128629