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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
An Open-label Extension Study to Evaluate Long-term Efficacy and Safety of Odevixibat in Children With Biliary AtresiaCongenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Abnormalities, Digestive System Diseases, bile duct disorder, biliary atresia, biliary tract disorderActive, not recruitingPhase 32026-10-01NCT05426733
Newly-diagnosed Intermediate/High Risk Pediatric B-cell ALL ProtocolB-cell neoplasm, Burkitt lymphoma, DNA Virus Infections, Epstein-Barr virus infection, Hemic and Lymphatic Diseases, Herpesviridae infectious disease, Infections, Neoplasms by Histologic Type, Precursor Cell Lymphoblastic Leukemia-Lymphoma, Tumor Virus Infections, hematologic disorder, immune system disorder, immunoproliferative disorder, leukemia, lymphatic system disorder, lymphoid leukemia, lymphoma, lymphoproliferative syndrome, neoplasm, viral infectious diseaseRecruitingPhase 2 / Phase 32026-07-23NCT06764238
Effects of Intermittent Dietary Restriction on Cardiometabolic Risk in School-aged ChildrenInsulin Resistance, Nutritional and Metabolic Diseases, glucose metabolism disease, hyperinsulinism, metabolic disease, metabolic syndrome XRecruitingNot applicable2026-07-06NCT06500078
Close Loop Smart Weaning for INO With PPHNCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Infant, Newborn, Diseases, lung disorder, persistent fetal circulation syndrome, pulmonary hypertension, respiratory system disorderRecruitingNot applicable2026-05-13NCT06832163
Development of Prosocial Behaviors and Related Brain Network in Infants of High and Low Risk of ASDautism, autism spectrum disorder, neurodevelopmental disorder, pervasive developmental disorder, psychiatric disorderRecruitingNot stated2026-03-16NCT06329245
YTS109 in Pediatric Relapsed/Refractory Autoimmune DiseasesSjogren syndrome, Skin and Connective Tissue Diseases, Stomatognathic Diseases, Xerostomia, anti-neutrophil cytoplasmic antibody-associated vasculitis, antiphospholipid syndrome, arthritic joint disease, arthropathy, autoimmune disease, cardiovascular disorder, connective tissue disorder, diffuse scleroderma, dry eye syndrome, eye disorder, immune system disorder, lacrimal apparatus disorder, mouth disorder, muscle tissue disorder, musculoskeletal system disorder, myositis disease, necrotizing vasculitis, nervous system disorder, neuromuscular disease, rheumatic disorder, rheumatoid arthritis, salivary gland disorder, skin disorder, skin vascular disease, systemic lupus erythematosus, systemic sclerosis, vascular disorder, vasculitisNot yet recruitingPhase 12026-02-27NCT07439029
Differences in Prosocial Behaviors and Related Brain Networks in Children With Autism and Typical Developmentautism, autism spectrum disorder, neurodevelopmental disorder, pervasive developmental disorder, psychiatric disorderRecruitingNot stated2025-05-29NCT06908174
Clinical Study on Strategy for Refractory Henoch-Schönlein PurpuraHemic and Lymphatic Diseases, Hemorrhage, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Signs and Symptoms, Skin Manifestations, Skin and Connective Tissue Diseases, blood coagulation disease, cardiovascular disorder, hematologic disorder, hemorrhagic disease, immune system disorder, immunoglobulin A vasculitis, purpura, skin disorder, skin vascular disease, type III hypersensitivity disease, vascular disorder, vascular hemostatic disease, vasculitisRecruitingNot applicable2025-02-19NCT03647852
Clinical Cohort Study of DHA in Neurodevelopmental Disordersautism, autism spectrum disorder, neurodevelopmental disorder, pervasive developmental disorder, psychiatric disorderActive, not recruitingNot applicable2025-02-18NCT05841927
Evaluation of the Safety, Tolerability and Efficacy of a Gene Therapy Drug for the Treatment of Pediatric Fabry DiseaseBrain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Cerebral Small Vessel Diseases, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Fabry disease, Lipid Metabolism Disorders, Lipid Metabolism, Inborn Errors, Lysosomal Storage Diseases, Nervous System, Nutritional and Metabolic Diseases, X-linked disease, brain disorder, cardiovascular disorder, central nervous system disorder, cerebrovascular disorder, hereditary disease, inborn errors of metabolism, lysosomal lipid storage disorder, lysosomal storage disease, metabolic disease, nervous system disorder, sphingolipidosis, vascular disorderRecruitingEarly phase 12024-07-09NCT06207552