Hôpital Necker - Enfants Malades APHP
Hôpital Necker - Enfants Malades APHP
Paris, France1 results · Page 1 of 1
Clinical trials
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| Trial | Conditions | Status | Phase | Updated | More info | NCT ID |
|---|---|---|---|---|---|---|
| An Extension Study to Evaluate the Long-Term Safety and Clinical Activity of mRNA-3705 in Participants Previously Enrolled in Other Clinical Studies of mRNA-3705 | Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Nutritional and Metabolic Diseases, hereditary disease, inborn errors of metabolism, metabolic disease, methylmalonic acidemia | Recruiting | Phase 1 / Phase 2 | 2025-12-23 | NCT05295433 |