University of Cagliari, Ospedale Pediatrico Microcitemico, via Jenner sn, 09121 Cagliari -
University of Cagliari, Ospedale Pediatrico Microcitemico, via Jenner sn, 09121 Cagliari -
Cagliari, CA, Italy1 results ยท Page 1 of 1
Clinical trials
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| Trial | Conditions | Status | Phase | Updated | More info | NCT ID |
|---|---|---|---|---|---|---|
| Study to Evaluate the Long- Term Safety and Efficacy of Luspatercept in Subjects Who Received at Least One Dose of Luspatercept in the Compassionate Use Phase | Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, Thalassemia Major, anemia, beta thalassemia, familial hemolytic anemia, hematologic disorder, hemolytic anemia, hereditary disease, inherited hemoglobinopathy, thalassemia | Active, not recruiting | Not stated | 2025-04-06 | NCT06913634 |