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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
A Study Evaluating the Efficacy and Safety of Mitapivat (AG-348) in Participants With Sickle Cell Disease (RISE UP)Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, anemia, familial hemolytic anemia, hematologic disorder, hemolytic anemia, hereditary disease, inherited hemoglobinopathy, sickle cell diseaseActive, not recruitingPhase 2 / Phase 32026-06-23NCT05031780
A Study of mRNA-3745 in Adult and Pediatric Participants With Glycogen Storage Disease Type 1a (GSD1a)Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Nutritional and Metabolic Diseases, disorder of glycogen metabolism, glucose metabolism disease, glycogen storage disease I, hereditary disease, inborn carbohydrate metabolic disorder, inborn errors of metabolism, metabolic diseaseActive, not recruitingPhase 1 / Phase 22025-12-15NCT05095727