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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Evaluation of MiniMed Next Generation Extended Wear Sensors and Algorithm in Patients With Type 1 and Type 2 DiabetesNutritional and Metabolic Diseases, autoimmune disease, diabetes mellitus, endocrine system disorder, glucose metabolism disease, immune system disorder, metabolic disease, type 1 diabetes mellitus, type 2 diabetes mellitusRecruitingNot applicable2026-10-07NCT07864168
Phase 2 Study of SAT-3247 in Pediatric Ambulatory PatientsCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne muscular dystrophy, Muscular Disorders, Atrophic, X-linked disease, hereditary disease, muscle tissue disorder, muscular dystrophy, musculoskeletal system disorder, nervous system disorder, neuromuscular diseaseActive, not recruitingPhase 22026-10-02NCT07287189
Study to Learn More About the Safety and Effectiveness of the Drug VITRAKVI During Routine Use in Patients With TRK Fusion Cancer Which is Locally Advanced or Spread From the Place Where it Started to Other Places in the BodyLocally Advanced or Metastatic Solid Tumor Harboring an NTRK Gene FusionRecruitingNot stated2026-10-02NCT04142437
Liothyronine in Combination With BIT Regimen for Medulloblastoma With or Without Minimal Residual DiseaseMedulloblastoma, Childhood, Neoplasms by Histologic Type, Neoplasms, Germ Cell and Embryonal, Neoplasms, Nerve Tissue, Neuroectodermal Tumors, Primitive, epithelial neoplasm, glioma, medulloblastoma, neoplasm, neuroepithelial neoplasm, primitive neuroectodermal tumorRecruitingPhase 1 / Phase 22026-09-28NCT07346157
High vs.Standard Dose Influenza Vaccine in Pediatric Solid Organ Transplant (SOT) RecipientsDisease Attributes, Infections, Pathologic Processes, Pathological Conditions, Signs and Symptoms, RNA Virus Infections, infectious disease, influenza, respiratory system disorder, respiratory tract infectious disorder, viral infectious diseaseRecruitingPhase 22026-09-24NCT05947071
The PRISM-Social Needs (PRISM-SN) Intervention for Adolescents and Young Adults With Cancercancer, neoplasmActive, not recruitingNot applicable2026-09-09NCT06242964
GATEWAY: Safety Evaluation of the MiniMed™ NMX8-AID System in Children and Adults Living With DiabetesNutritional and Metabolic Diseases, autoimmune disease, diabetes mellitus, endocrine system disorder, glucose metabolism disease, immune system disorder, metabolic disease, type 1 diabetes mellitus, type 2 diabetes mellitusActive, not recruitingNot applicable2026-09-02NCT07228117
A Study of Deramiocel (CAP-1002) in Ambulatory and Non-Ambulatory Patients With Duchenne Muscular DystrophyCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne muscular dystrophy, Muscular Disorders, Atrophic, X-linked disease, hereditary disease, muscle tissue disorder, muscular dystrophy, musculoskeletal system disorder, nervous system disorder, neuromuscular diseaseActive, not recruitingPhase 32026-08-28NCT05126758
Modeling Mortality in Duchenne Muscular Dystrophy Cardiomyopathy: Identification of Surrogate Outcome Measures for DMD Drug TrialsBecker muscular dystrophy, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne muscular dystrophy, Muscular Disorders, Atrophic, X-linked disease, cardiomyopathy, cardiovascular disorder, heart disorder, hereditary disease, muscle tissue disorder, muscular dystrophy, musculoskeletal system disorder, nervous system disorder, neuromuscular diseaseRecruitingNot stated2026-07-28NCT07674758
Study to Evaluate the Safety and Efficacy of PF-06939926 for the Treatment of Duchenne Muscular DystrophyCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne muscular dystrophy, Muscular Disorders, Atrophic, X-linked disease, hereditary disease, muscle tissue disorder, muscular dystrophy, musculoskeletal system disorder, nervous system disorder, neuromuscular diseaseActive, not recruitingPhase 32026-07-22NCT04281485
Family Bridge ProgramGeneral Pediatric Medical Conditions; Health Disparities; Healthcare System Navigation; Patient-provider CommunicationEnrolling by invitationNot applicable2026-06-15NCT06276621
VITAS: Atezolizumab in Combination With Chemotherapy for Pediatric Relapsed/Refractory Solid TumorsMyosarcoma, Neoplasms by Histologic Type, Neoplasms, Connective and Soft Tissue, myomatous neoplasm, neoplasm, rhabdomyosarcoma, sarcomaRecruitingPhase 1 / Phase 22026-06-02NCT04796012
Improving Continuous Renal Replacement Therapy Outcomes in Neonates and Infants Through Interdisciplinary CollaborationChronic Disease, Chronic Kidney Diseases, Disease Attributes, Female Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Male Urogenital Diseases, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Urogenital Diseases, acute kidney injury, chronic renal failure syndrome, kidney disorder, kidney failure, urinary system disorderEnrolling by invitationNot stated2026-03-23NCT05161078
Mobile Video Interpretation to Optimize Communication Across Language BarriersLimited English ProficiencyActive, not recruitingNot applicable2026-01-23NCT05591586
InvesT1D: Promoting Adolescent Investment in Diabetes CareNutritional and Metabolic Diseases, autoimmune disease, diabetes mellitus, endocrine system disorder, glucose metabolism disease, immune system disorder, metabolic disease, type 1 diabetes mellitusRecruitingNot applicable2025-12-16NCT06384911
Optimal Ventilation for Cardiac Arrestcardiac arrest, cardiovascular disorder, heart disorderRecruitingNot applicable2025-10-08NCT07114510
Open-Label Extension Study of DCCR in Patients With Prader-Willi SyndromeAbnormalities, Multiple, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Imprinting Disorders, Neurobehavioral Manifestations, Neurologic Manifestations, Nutritional and Metabolic Diseases, Overweight, Prader-Willi syndrome, chromosomal disorder, hereditary disease, intellectual disability, nervous system disorder, nutritional disorder, obesity disorder, overnutritionActive, not recruitingPhase 32025-04-02NCT05701774
Percutaneous Intervention Versus Observational Trial of Arterial Ductus in Low Weight InfantsCardiovascular Abnormalities, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, cardiovascular disorder, congenital heart disease, heart disorder, patent ductus arteriosusRecruitingNot applicable2025-03-30NCT05547165
Registry of Patients With a Diagnosis of Spinal Muscular Atrophy (SMA)central nervous system disorder, motor neuron disorder, nervous system disorder, neurodegenerative disease, neuromuscular disease, spinal cord disorder, spinal muscular atrophyRecruitingNot stated2025-01-31NCT04174157
Situation Awareness Incorporating Multidisciplinary Teams Reduce Arrests In the Pediatric ICUcardiac arrest, cardiovascular disorder, heart disorderActive, not recruitingNot applicable2024-08-16NCT06553534
The Tether™ - Vertebral Body Tethering System Post Approval StudyScoliosis IdiopathicRecruitingNot stated2024-02-22NCT04505579