21 results · Page 1 of 1

Swipe the table sideways for more columns.

TrialConditionsStatusPhaseUpdatedMore infoNCT ID
A Study Evaluating the Long-term Safety and Efficacy of VX-121 Combination TherapyCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, Infant, Newborn, Diseases, cystic fibrosis, hereditary disease, lung disorder, pancreas disorder, respiratory system disorderActive, not recruitingPhase 32026-10-09NCT05444257
Study to Evaluate Elexacaftor/Tezacaftor/Ivacaftor (ELX/TEZ/IVA) Long-term Safety and Efficacy in Subjects Without F508delCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, Infant, Newborn, Diseases, cystic fibrosis, hereditary disease, lung disorder, pancreas disorder, respiratory system disorderActive, not recruitingPhase 32026-10-09NCT05331183
Follow-up in Gynecological Cancer Survivorsfemale reproductive organ cancerActive, not recruitingNot stated2026-10-07NCT03515993
Study of SRP-1003 in Participants With Type 1 Myotonic DystrophyCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Muscular Disorders, Atrophic, hereditary disease, inherited neurodegenerative disorder, muscle tissue disorder, muscular dystrophy, musculoskeletal system disorder, myotonic dystrophy, myotonic syndrome, nervous system disorder, neurodegenerative disease, neuromuscular diseaseEnrolling by invitationPhase 1 / Phase 22026-10-05NCT06138743
Open Label Extension to Assess Long Term Safety and Efficacy of KL1333 in Patients With Primary Mitochondrial DiseaseNutritional and Metabolic Diseases, inborn mitochondrial metabolism disorder, metabolic diseaseRecruitingPhase 22026-09-16NCT07514338
Neurovascular Product Surveillance RegistryAneurysm, brain aneurysm, brain disorder, cardiovascular disorder, central nervous system disorder, cerebrovascular disorder, intracranial arterial disease, ischemic stroke, nervous system disorder, stroke disorder, vascular disorderRecruitingNot stated2026-09-15NCT02988128
Interfant-21 Treatment Protocol for Infants Under 1 Year With KMT2A-rearranged ALL or Mixed Phenotype Acute LeukemiaHemic and Lymphatic Diseases, Neoplasms by Histologic Type, Precursor Cell Lymphoblastic Leukemia-Lymphoma, acute biphenotypic leukemia, hematologic disorder, immune system disorder, immunoproliferative disorder, leukemia, lymphatic system disorder, lymphoid leukemia, lymphoproliferative syndrome, mixed phenotype acute leukemia, neoplasmRecruitingPhase 32026-07-10NCT05327894
Study of Tinengotinib VS. Physician's Choice a Treatment of Subjects With FGFR-altered in CholangiocarcinomaNeoplasms by Histologic Type, adenocarcinoma, carcinoma, cholangiocarcinoma, epithelial neoplasm, neoplasmActive, not recruitingPhase 32026-07-06NCT05948475
Efficacy of KL1333 in Adult Patients With Primary Mitochondrial DiseaseMuscle Weakness, Neurologic Manifestations, Neuromuscular Manifestations, Nutritional and Metabolic Diseases, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Signs and Symptoms, diabetes mellitus, endocrine system disorder, glucose metabolism disease, metabolic disease, muscle tissue disorder, musculoskeletal system disorder, nervous system disorder, neuromuscular diseaseRecruitingPhase 22026-06-26NCT05650229
A Phase 3 Trial of Epcoritamab vs Investigator's Choice Chemotherapy in Relapsed/Refractory (R/R) Diffuse Large B-cell Lymphoma (DLBCL)B-cell neoplasm, Hemic and Lymphatic Diseases, Neoplasms by Histologic Type, diffuse large B-cell lymphoma, immune system disorder, immunoproliferative disorder, lymphatic system disorder, lymphoma, lymphoproliferative syndrome, neoplasmActive, not recruitingPhase 32026-05-22NCT04628494
Efficacy and Safety of Obefazimod in Subjects With Moderately to Severely Active Crohn's DiseaseCrohn disease, Digestive System Diseases, digestive system disorder, gastroenteritis, inflammatory bowel disease, intestinal disorderRecruitingPhase 22026-04-27NCT06456593
Safety and Efficacy of Quizartinib in Children and Young Adults With Acute Myeloid Leukemia (AML), a Cancer of the BloodDisease Attributes, Hemic and Lymphatic Diseases, Neoplasms by Histologic Type, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Recurrence, acute myeloid leukemia, hematologic disorder, leukemia, myeloid leukemia, neoplasmActive, not recruitingPhase 1 / Phase 22026-04-01NCT03793478
Assess Safety and Efficacy of VAD044 in HHT PatientsCardiovascular Abnormalities, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, arteriovenous hemangioma/malformation, cardiovascular disorder, hematologic disorder, hemorrhagic disease, hereditary hemorrhagic telangiectasia, telangiectasis, vascular disorder, vascular hemostatic disease, vascular malformationActive, not recruitingPhase 1 / Phase 22026-03-17NCT05406362
Phase 1/2 Study of IMC-R117C in Selected Advanced Cancerscancer, neoplasmRecruitingPhase 1 / Phase 22026-01-28NCT06840119
Breast Implant-associated Anaplastic Large Cell Lymphoma (BIA-ALCL) RegistryAnaplastic Large Cell Lymphoma Associated With Breast Implants (BIA-ALCL)RecruitingNot stated2026-01-14NCT04220970
Motiva Flora® Aesthetic Breast Recon® Clinical StudyBone Diseases, Developmental, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Limb Deformities, Congenital, Musculoskeletal Abnormalities, Neoplasms by Site, Poland syndrome, Skin and Connective Tissue Diseases, bone disorder, breast cancer, breast disorder, breast neoplasm, dysostosis, musculoskeletal system disorder, neoplasm, skin disorder, syndactyly, synostosisRecruitingNot applicable2025-11-26NCT06146231
OligoCare TwiCs (Trials Within Cohorts) Trial Comparing Acute Toxicity in Single-fraction vs Multiple-fraction SBRT for Metastasis-directed Treatment (SPRINT)Digestive System Diseases, Digestive System Neoplasms, Genital Diseases, Male Urogenital Diseases, Neoplasms by Site, Skin and Connective Tissue Diseases, Urogenital Diseases, Urogenital Neoplasms, breast cancer, breast disorder, breast neoplasm, colonic disorder, colorectal cancer, colorectal neoplasm, digestive system disorder, digestive system neoplasm, intestinal disorder, male reproductive organ cancer, male reproductive system disorder, neoplasm, non-small cell lung carcinoma, prostate cancer, prostate disorder, rectal disorder, skin disorderRecruitingNot applicable2025-08-01NCT06462963
Oral Pooled Fecal Microbiotherapy to Prevent Allogeneic Hematopoietic Cell Transplantation Complications (PHOEBUS Trial)Transplant ComplicationRecruitingPhase 22024-12-27NCT05762211
MaaT013 As Salvage Therapy in Ruxolitinib Refractory GI-aGVHD PatientsAcute Graft Versus Host Disease in Intestine; Steroid Refractory GVHDActive, not recruitingPhase 32024-10-17NCT04769895
Subcutaneous Infliximab After A Previous Intravenous Dose OptimizationCrohn disease, Digestive System Diseases, colitis, colonic disorder, digestive system disorder, gastroenteritis, inflammatory bowel disease, intestinal disorder, ulcerative colitisRecruitingPhase 42024-07-26NCT06113913
FaR-RMS: An Overarching Study for Children and Adults With Frontline and Relapsed RhabdoMyoSarcomaMyosarcoma, Neoplasms by Histologic Type, Neoplasms, Connective and Soft Tissue, myomatous neoplasm, neoplasm, rhabdomyosarcoma, sarcomaRecruitingPhase 1 / Phase 22024-05-23NCT04625907