7 results ยท Page 1 of 1

Swipe the table sideways for more columns.

TrialConditionsStatusPhaseUpdatedMore infoNCT ID
A Single Ascending Dose Study to Assess the Safety, Tolerability, Pharmacokinetics and Pharmacodynamics of CITY-FXI in Healthy Adults, Adults With FV Leiden or Prothrombin G20210A Mutation, and Adults With a History of Provoked Venous ThromboembolismEmbolism and Thrombosis, Thromboembolism, cardiovascular disorder, vascular disorder, venous thromboembolismRecruitingPhase 12026-09-25NCT07430397
A Safety and Tolerability Trial Evaluating CTX310 in Participants With Refractory DyslipidemiasCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Dyslipidemias, Hypercholesterolemia, Lipid Metabolism Disorders, Lipid Metabolism, Inborn Errors, Nutritional and Metabolic Diseases, familial hypercholesterolemia, hereditary disease, homozygous familial hypercholesterolemia, hyperlipidemia, hyperlipoproteinemia, hyperlipoproteinemia type V, hypertriglyceridemia, inborn errors of metabolism, metabolic diseaseRecruitingPhase 12026-09-18NCT07491172
Phase 1 Study of ADX-626 in Healthy ParticipantsHealthy Adult ParticipantsRecruitingPhase 12026-09-10NCT07081503
A Research Study on the Effects of NNC0537-1482 in Participants With Heart Failurecardiovascular disorder, heart disorder, heart failureRecruitingPhase 12026-09-01NCT07218627
A Study Assessing HMB-002 in Participants With Von Willebrand DiseaseCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, blood coagulation disease, blood platelet disease, coagulation protein disease, hematologic disorder, hemorrhagic disease, hereditary disease, inherited blood coagulation disorder, von Willebrand disease (hereditary or acquired), von Willebrand disease 3RecruitingPhase 1 / Phase 22026-06-30NCT06754852
A Study of Bleeding and Treatment in Participants With Von Willebrand DiseaseCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, blood coagulation disease, blood platelet disease, coagulation protein disease, hematologic disorder, hemorrhagic disease, hereditary disease, inherited blood coagulation disorder, von Willebrand disease (hereditary or acquired), von Willebrand disease 2, von Willebrand disease 3, von Willebrand disease type 2A, von Willebrand disease type 2M, von Willebrand disease type 2NRecruitingNot stated2026-04-21NCT06610201
An Extension Study to Assess Long-Term Safety of Eplontersen in Adults With Transthyretin-Mediated Amyloid Cardiomyopathy (ATTR-CM)Nutritional and Metabolic Diseases, amyloidosis, metabolic disease, proteostasis deficienciesEnrolling by invitationPhase 32026-04-17NCT05667493