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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
A Study of MZE782 in Adults With PKUBrain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Nutritional and Metabolic Diseases, brain disorder, central nervous system disorder, hereditary disease, inborn disorder of amino acid metabolism, inborn errors of metabolism, metabolic disease, nervous system disorder, phenylketonuriaRecruitingPhase 22026-10-08NCT07694440
WiTNNess - TNNT1 Myopathy Natural History Studycongenital structural myopathy, hereditary skeletal muscle disorder, muscle tissue disorder, musculoskeletal system disorder, nemaline myopathy, nemaline myopathy 5, nervous system disorder, neuromuscular diseaseRecruitingNot stated2026-06-23NCT06374719