Stollery Children's Hospital University of Alberta
Stollery Children's Hospital University of Alberta
Edmonton, Alberta, Canada3 results ยท Page 1 of 1
Clinical trials
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| Trial | Conditions | Status | Phase | Updated | More info | NCT ID |
|---|---|---|---|---|---|---|
| Open-Label Study of mRNA-3927 in Participants With Propionic Acidemia | Acid-Base Imbalance, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Nutritional and Metabolic Diseases, acidosis disorder, hereditary disease, inborn disorder of amino acid metabolism, inborn errors of metabolism, metabolic disease, propionic acidemia | Recruiting | Phase 1 / Phase 2 | 2026-01-22 | NCT04159103 | |
| An Extension Study to Evaluate the Long-Term Safety and Clinical Activity of mRNA-3705 in Participants Previously Enrolled in Other Clinical Studies of mRNA-3705 | Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Nutritional and Metabolic Diseases, hereditary disease, inborn errors of metabolism, metabolic disease, methylmalonic acidemia | Recruiting | Phase 1 / Phase 2 | 2025-12-23 | NCT05295433 | |
| A Study of mRNA-3745 in Adult and Pediatric Participants With Glycogen Storage Disease Type 1a (GSD1a) | Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Nutritional and Metabolic Diseases, disorder of glycogen metabolism, glucose metabolism disease, glycogen storage disease I, hereditary disease, inborn carbohydrate metabolic disorder, inborn errors of metabolism, metabolic disease | Active, not recruiting | Phase 1 / Phase 2 | 2025-12-15 | NCT05095727 |