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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
A Study of the Safety and Efficacy of Prime Editing (PM577) in Participants With Wilson Disease (WD)Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, Nutritional and Metabolic Diseases, Wilson disease, basal ganglia disorder, brain disorder, central nervous system disorder, hereditary disease, inborn errors of metabolism, inborn metal metabolism disorder, inherited neurodegenerative disorder, liver disorder, metabolic disease, movement disorder, nervous system disorder, neurodegenerative diseaseRecruitingPhase 1 / Phase 22026-10-01NCT07748403