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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Campath/Fludarabine/Melphalan Transplant Conditioning for Non-Malignant DiseasesCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, Nutritional and Metabolic Diseases, hematologic disorder, hereditary disease, inherited hemoglobinopathy, metabolic diseaseRecruitingPhase 1 / Phase 22026-09-16NCT00920972
Modeling Mortality in Duchenne Muscular Dystrophy Cardiomyopathy: Identification of Surrogate Outcome Measures for DMD Drug TrialsBecker muscular dystrophy, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne muscular dystrophy, Muscular Disorders, Atrophic, X-linked disease, cardiomyopathy, cardiovascular disorder, heart disorder, hereditary disease, muscle tissue disorder, muscular dystrophy, musculoskeletal system disorder, nervous system disorder, neuromuscular diseaseRecruitingNot stated2026-07-28NCT07674758
Comparison of Uncomplicated Candidemia Therapy Duration in ChildrenBacterial Infections and Mycoses, Infections, Invasive Fungal Infections, candidiasis, candidiasis, invasive, fungal infectious diseaseRecruitingNot applicable2026-04-17NCT05763251
Improving Safety and Quality of Tracheal Intubation Practice in Pediatric ICUsFailed or Difficult Intubation, Sequela; Intubation Complication; Intubation; DifficultRecruitingNot stated2026-01-09NCT02493478
Oral Pyridoxal 5'-Phosphate for the Treatment of Patients With PNPO DeficiencyPyridox(am)Ine 5'-Phosphate Oxidase DeficiencyRecruitingPhase 32025-10-16NCT04706013