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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Comprehensive Program for Hereditary Transthyretin AmyloidosisCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Nutritional and Metabolic Diseases, amyloidosis, hereditary amyloidosis, hereditary disease, inborn errors of metabolism, metabolic disease, proteostasis deficienciesRecruitingNot stated2026-03-24NCT07213297