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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
A Phase I/II Clinical Study to Evaluate SKG0201 Injection in Subjects With Spinal Muscular Atrophy Type ICongenital, Hereditary, and Neonatal Diseases and Abnormalities, Spinal Muscular Atrophies of Childhood, Spinal Muscular Atrophy Type I, central nervous system disorder, hereditary disease, inherited neurodegenerative disorder, motor neuron disorder, nervous system disorder, neurodegenerative disease, neuromuscular disease, spinal cord disorder, spinal muscular atrophyRecruitingPhase 1 / Phase 22026-08-26NCT07554924
Zuberitamab in the First Episode of Paediatric Nephrotic SyndromeFemale Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Male Urogenital Diseases, Urogenital Diseases, kidney disorder, nephrosis, nephrotic syndrome, urinary system disorderNot yet recruitingPhase 32026-08-14NCT07765914
Childhood-onset Lupus Nephritis Initial Glucocorticoid-dose Harmonization Trial (LIGHT Trial)Female Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Male Urogenital Diseases, Skin and Connective Tissue Diseases, Urogenital Diseases, autoimmune disease, connective tissue disorder, glomerulonephritis, immune system disorder, kidney disorder, lupus nephritis, nephritis, systemic lupus erythematosus, urinary system disorderRecruitingPhase 42026-07-22NCT07719140
A Phase III Clinical Study to Evaluate the Efficacy, Safety, and Tolerability of Plonmarlimab in Subjects With Relapsed/Refractory Rheumatic and Immunologic Disease-associated Haemophagocytic Lymphohistiocytosis (Also Known as Macrophage Activation Syndrome [MAS])Disease Attributes, Pathologic Processes, Pathological Conditions, Signs and Symptoms, RecurrenceRecruitingPhase 32026-07-20NCT07208058
The Intervention of Obesity in Children With Prader-Willi Syndrome Using Prebiotics and ProbioticsAbnormalities, Multiple, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Imprinting Disorders, Neurobehavioral Manifestations, Neurologic Manifestations, Nutritional and Metabolic Diseases, Overweight, Prader-Willi syndrome, chromosomal disorder, hereditary disease, intellectual disability, nervous system disorder, nutritional disorder, obesity disorder, overnutritionRecruitingNot applicable2026-07-06NCT05791604
Chinese Multicenter Clinical Outcome Cohort Study of Myotonic Dystrophy Type 1 (C-DMCOS-DM1)Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Muscular Disorders, Atrophic, hereditary disease, inherited neurodegenerative disorder, muscle tissue disorder, muscular dystrophy, musculoskeletal system disorder, myotonic dystrophy, myotonic syndrome, nervous system disorder, neurodegenerative disease, neuromuscular diseaseEnrolling by invitationNot stated2026-06-02NCT06101940
A Phase 2 Safety and Efficacy Study Evaluating CS-101 in Participants With β-Thalassemia Majorβ-thalassemia MajorNot yet recruitingPhase 22026-03-24NCT07489196
Intervention for Children With Type 1 Diabetes Targeting Gut MicrobesNutritional and Metabolic Diseases, autoimmune disease, diabetes mellitus, endocrine system disorder, glucose metabolism disease, immune system disorder, metabolic disease, type 1 diabetes mellitusRecruitingNot applicable2026-03-17NCT06198725
Cyclophosphamide in the Treatment of Associated Acquired Lipodystrophy Syndrome With Type 1 DiabetesLipodystrophy Acquired; Type1diabetesActive, not recruitingNot applicable2026-03-17NCT03936829
Sequential Transplantation of UCBSCs and Islet Cells in Children and Adolescents With Monogenic Immunodeficiency T1DMNutritional and Metabolic Diseases, autoimmune disease, diabetes mellitus, endocrine system disorder, glucose metabolism disease, immune system disorder, inborn error of immunity, metabolic disease, type 1 diabetes mellitusRecruitingNot applicable2026-03-17NCT03835312
Treatment Strategy of Human Gamma Globulin on the Therapy for Intensively Ill Children With Inflammatory StormCritical Illness, Disease Attributes, Infections, Inflammation, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Sepsis, Severe Sepsis, Systemic Inflammatory Response SyndromeRecruitingNot stated2026-03-16NCT04850456
ECMO Treatment of Children in China in the Past 10 YearsChild, Only; Extracorporeal Membrane OxygenationRecruitingNot stated2026-03-16NCT04709432
Risk Factors for Colonization or Infection With Carbapenem-Resistant Enterobacteriaceae in ChildrenCarbapenem-Resistant Enterobacteriaceae InfectionRecruitingNot stated2026-03-16NCT04535661
Application of Early Bundle Management of Mechanical Ventilation to Prevent Ventilator Dependence in ChildrenProlonged Mechanical VentilationRecruitingNot applicable2026-02-17NCT06125210
Chinese PICU Collaborative Network on Pathogens and Drug Resistance of Severe InfectionsInfectionsRecruitingNot stated2026-02-17NCT04923828
Newly-diagnosed Pediatric Ph-positive B-ALL ProtocolHemic and Lymphatic Diseases, Neoplasms by Histologic Type, Precursor Cell Lymphoblastic Leukemia-Lymphoma, hematologic disorder, immune system disorder, immunoproliferative disorder, leukemia, lymphatic system disorder, lymphoid leukemia, lymphoproliferative syndrome, neoplasmRecruitingPhase 32025-09-03NCT07152041
Newly-diagnosed Low Risk Pediatric B-cell ALL ProtocolB-cell neoplasm, Burkitt lymphoma, DNA Virus Infections, Epstein-Barr virus infection, Hemic and Lymphatic Diseases, Herpesviridae infectious disease, Infections, Neoplasms by Histologic Type, Precursor Cell Lymphoblastic Leukemia-Lymphoma, Tumor Virus Infections, hematologic disorder, immune system disorder, immunoproliferative disorder, leukemia, lymphatic system disorder, lymphoid leukemia, lymphoma, lymphoproliferative syndrome, neoplasm, viral infectious diseaseRecruitingPhase 2 / Phase 32025-08-26NCT06882057
Newly-diagnosed Pediatric T-cell ALL ProtocolHemic and Lymphatic Diseases, Neoplasms by Histologic Type, Precursor Cell Lymphoblastic Leukemia-Lymphoma, Precursor T-Cell Lymphoblastic Leukemia-Lymphoma, hematologic disorder, immune system disorder, immunoproliferative disorder, leukemia, lymphatic system disorder, lymphoid leukemia, lymphoproliferative syndrome, neoplasmRecruitingPhase 2 / Phase 32025-08-26NCT06855810
Clinical Study of Pegylated Somatropin (PEG Somatropin) to Treat SGA Children With Short StatureShort Stature Children Born Small for Gestational Age (SGA)Active, not recruitingPhase 22025-05-25NCT02375620
Study on Early Genetic Screening and Precise Strategy of Neonatal Critical IllnessCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Death, Female Urogenital Diseases and Pregnancy Complications, Fetal Death, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Urogenital Diseases, hereditary disease, pregnancy disorder, pregnancy disorder with abortive outcomeRecruitingNot stated2025-02-20NCT04905537