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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Pediatric Down Syndrome Post-Approval StudyAbnormalities, Multiple, Apnea, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Down syndrome, Dyssomnias, Neurobehavioral Manifestations, Neurologic Manifestations, Respiration Disorders, Sleep Disorders, Intrinsic, chromosomal disorder, hereditary disease, intellectual disability, nervous system disorder, obstructive sleep apnea syndrome, respiratory system disorder, sleep apnea syndrome, sleep-wake disorderRecruitingNot applicable2025-02-28NCT06851338
International CDKL5 Clinical Research Networkcraniodiaphyseal dysplasia, autosomal dominantRecruitingNot stated2023-12-06NCT05558371
Study of Gene Modified Donor T-cells Following TCR Alpha Beta Positive Depleted Stem Cell TransplantBone Diseases, Developmental, Bone Marrow Failure Disorders, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Cytopenia, Hemic and Lymphatic Diseases, Neoplasms by Histologic Type, Neoplasms by Site, Precursor Cell Lymphoblastic Leukemia-Lymphoma, Primary Immunodeficiency Diseases, acute myeloid leukemia, anemia, aplastic anemia, bone disorder, bone marrow disorder, hematologic disorder, hematopoietic and lymphoid system neoplasm, hereditary disease, immune system disorder, immunoproliferative disorder, inborn error of immunity, leukemia, lymphatic system disorder, lymphoid leukemia, lymphoma, lymphoproliferative syndrome, musculoskeletal system disorder, myelodysplastic syndrome, myeloid leukemia, neoplasm, osteochondrodysplasia, osteopetrosis, osteosclerosisActive, not recruitingPhase 1 / Phase 22022-07-12NCT03301168