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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
A Study Evaluating the Long-Term Efficacy and Safety of Ralinepag in Subjects With PAH Via an Open-Label ExtensionFamilial Primary Pulmonary Hypertension, Skin and Connective Tissue Diseases, cardiovascular disorder, connective tissue disorder, hypertensive disorder, lung disorder, pulmonary arterial hypertension, pulmonary hypertension, respiratory system disorder, vascular disorderEnrolling by invitationPhase 32026-10-06NCT03683186
A Study of BIIB067 (Tofersen) Initiated in Clinically Presymptomatic Adults With a Confirmed Superoxide Dismutase 1 MutationAmyotrophic Lateral Sclerosis Associated With a SOD1 Gene MutationActive, not recruitingPhase 32026-03-30NCT04856982