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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
A Retrospective Study to Characterize Participants With Propionic AcidemiaCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Nutritional and Metabolic Diseases, hereditary disease, inborn disorder of amino acid metabolism, inborn errors of metabolism, metabolic disease, propionic acidemiaRecruitingNot stated2026-02-05NCT05769621
Intraamniotic Administrations of ER004 to Male Subjects With X-linked Hypohidrotic Ectodermal DysplasiaAbnormalities, Multiple, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Ectodermal Dysplasia 1, Anhidrotic, Skin Abnormalities, Skin and Connective Tissue Diseases, X-linked disease, ectodermal dysplasia syndrome, hereditary disease, hereditary skin disorder, skin disorderRecruitingPhase 22025-04-30NCT04980638