Hôpital Necker - Enfants Malades
Hôpital Necker - Enfants Malades
Paris, Paris, France2 results · Page 1 of 1
Clinical trials
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| Trial | Conditions | Status | Phase | Updated | More info | NCT ID |
|---|---|---|---|---|---|---|
| A Retrospective Study to Characterize Participants With Propionic Acidemia | Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Nutritional and Metabolic Diseases, hereditary disease, inborn disorder of amino acid metabolism, inborn errors of metabolism, metabolic disease, propionic acidemia | Recruiting | Not stated | 2026-02-05 | NCT05769621 | |
| Intraamniotic Administrations of ER004 to Male Subjects With X-linked Hypohidrotic Ectodermal Dysplasia | Abnormalities, Multiple, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Ectodermal Dysplasia 1, Anhidrotic, Skin Abnormalities, Skin and Connective Tissue Diseases, X-linked disease, ectodermal dysplasia syndrome, hereditary disease, hereditary skin disorder, skin disorder | Recruiting | Phase 2 | 2025-04-30 | NCT04980638 |