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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
A Safety and Efficacy Study of hu14 in High-Risk Neuroblastoma PatientsHigh-Risk NeuroblastomaRecruitingPhase 2 / Phase 32026-10-08NCT07549321
CfDNA in Hereditary And High-risk Malignancies 2Adnexal Diseases, Colorectal Neoplasms, Hereditary Nonpolyposis, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, DNA repair disease, Digestive System Diseases, Digestive System Neoplasms, Female Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Genital Diseases, Li-Fraumeni syndrome, Neoplasms by Site, Nutritional and Metabolic Diseases, Skin and Connective Tissue Diseases, Urogenital Diseases, Urogenital Neoplasms, breast disorder, breast neoplasm, colonic disorder, colorectal neoplasm, digestive system disorder, digestive system neoplasm, endocrine system disorder, female reproductive system disorder, female reproductive system neoplasm, gastric neoplasm, gonadal disorder, hereditary breast ovarian cancer syndrome, hereditary disease, hereditary neoplastic syndrome, intestinal disorder, malignant endocrine neoplasm, metabolic disease, neoplasm, ovarian cancer, ovarian disorder, skin disorder, stomach disorderRecruitingNot stated2026-10-08NCT06726642
Real-World Effectiveness and Safety of Pegcetacoplan in Patients With C3G or IC-MPG: A Multi-Country StudyDisease Attributes, Female Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Male Urogenital Diseases, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Rare Diseases, Urogenital Diseases, glomerulonephritis, kidney disorder, nephritis, urinary system disorderRecruitingPhase 42026-09-09NCT07746895
Conditioning SCID Infants Diagnosed Earlysevere combined immunodeficiencyActive, not recruitingPhase 22026-08-28NCT03619551
Phase 1/2 Study of Mirdametinib + Vinblastine for Newly Diagnosed/Previously Untreated PLGG + Activation of MAPKPediatric Low-grade GliomaRecruitingPhase 1 / Phase 22026-08-11NCT06666348
ARDS in Children and ECMO Initiation Strategies Impact on Neurodevelopment (ASCEND)Respiration Disorders, adult acute respiratory distress syndrome, lung disorder, respiratory system disorderActive, not recruitingNot stated2026-07-14NCT05388708
Open-label, Long-term Safety, Efficacy, and Pharmacokinetics Study of Vibegron in Pediatric Subjects 2 Years to < 18 Years of Age With NDO and on CICCNS demyelinating autoimmune disease, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Hernia, Infections, Neoplasms by Site, Neuroinflammatory Diseases, Paraneoplastic Syndromes, Nervous System, Pathological Conditions, Anatomical, Pathological Conditions, Signs and Symptoms, acute transverse myelitis, autoimmune disease, autoimmune disorder of the nervous system, central nervous system disorder, central nervous system infectious disorder, central nervous system malformation, demyelinating disease, immune system disorder, injury, meningocele, myelitis, neoplasm, nervous system disorder, nervous system injury, neurodegenerative disease, paraneoplastic syndrome, spinal cord disorder, spinal cord injuryRecruitingPhase 2 / Phase 32026-06-15NCT05491525
A Study of Subcutaneous Blinatumomab Administration in Participants With R/R and MRD+ B-ALLDisease Attributes, Hemic and Lymphatic Diseases, Neoplasm, Residual, Neoplasms by Histologic Type, Neoplastic Processes, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Precursor Cell Lymphoblastic Leukemia-Lymphoma, Recurrence, hematologic disorder, immune system disorder, immunoproliferative disorder, leukemia, lymphatic system disorder, lymphoid leukemia, lymphoproliferative syndrome, neoplasmActive, not recruitingPhase 1 / Phase 22026-05-28NCT04521231
WeRoaM: Wearable Remote Monitoring in Heart Failurecardiovascular disorder, heart disorder, heart failureRecruitingNot stated2026-05-11NCT06969560
REduced-dose Steroid PrOtocol for Childhood Nephrotic SyndromE (RESPONSE)Female Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Male Urogenital Diseases, Nephrotic Syndrome, Minimal Change, Urogenital Diseases, focal segmental glomerulosclerosis, glomerulonephritis, kidney disorder, minimal change disease, nephritis, nephrosis, nephrotic syndrome, urinary system disorderActive, not recruitingPhase 32026-05-11NCT06635720
Complete Cognitive Intervention for cSLELupusRecruitingNot applicable2026-05-01NCT07302113
PromotIng Optimal Treatment for Community-acquired PNeumonia in EmErgency RoomsCommunity-Acquired Infections, Community-Acquired Pneumonia, Infections, lung disorder, pneumonia, respiratory system disorder, respiratory tract infectious disorderRecruitingNot applicable2026-04-29NCT07099976
Natural History Evaluation of Charcot Marie Tooth Disease (CMT) Types CMT1B, CMT2A, CMT4A, CMT4C, and OthersCharcot-Marie-Tooth disease, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, central nervous system malformation, hereditary disease, hereditary motor and sensory neuropathy, inherited neurodegenerative disorder, nervous system disorder, neurodegenerative disease, neuromuscular disease, peripheral nervous system disorder, polyneuropathyRecruitingNot stated2025-10-07NCT01193075
Be Sweet to Babies During NasolaryngoscopyInfant ConditionsRecruitingNot applicable2025-07-04NCT06641687
PROACT Pilot TrialKidney Transplant RejectionActive, not recruitingNot stated2025-06-15NCT06564649
Nemaline Myopathy Clinical Research Network (NM-CTRN)Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Thomsen and Becker disease, congenital structural myopathy, hereditary disease, inherited neurodegenerative disorder, muscle tissue disorder, musculoskeletal system disorder, myotonic syndrome, nemaline myopathy, nervous system disorder, neurodegenerative disease, neuromuscular diseaseNot yet recruitingNot stated2025-01-14NCT06774703
Non-Invasive Diagnosis of Pediatric Pulmonary Invasive Mold InfectionsBacterial Infections and Mycoses, Infections, Invasive Fungal Infections, Invasive Pulmonary Aspergillosis, aspergillosis, fungal infectious disease, fungal lung infectious disease, lung disorder, pulmonary aspergilloma, respiratory system disorderRecruitingNot stated2024-09-25NCT03827694
UCAN CAN-DU: Canada-Netherlands Personalized Medicine Network in Childhood Arthritis and Rheumatic DiseaseSkin and Connective Tissue Diseases, arthritic joint disease, arthropathy, autoimmune disease, connective tissue disorder, immune system disorder, juvenile idiopathic arthritis, musculoskeletal system disorder, rheumatic disorderRecruitingNot stated2024-08-19NCT06560606
KIdney aNd blooD prESsure ouTcomes in Childhood Cancer Survivors (CCS)Chronic Disease, Chronic Kidney Diseases, Disease Attributes, Female Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Male Urogenital Diseases, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Urogenital Diseases, acute kidney injury, cardiovascular disorder, childhood malignant neoplasm, chronic renal failure syndrome, hypertensive disorder, kidney disorder, kidney failure, neoplasm, urinary system disorder, vascular disorderRecruitingNot stated2024-04-17NCT06153147
Visual Telerehabilitation in Children, Adolescents and Young Adults With Hemianopsia Consecutive to a Brain TumourHemianopsia, Neurologic Manifestations, Pathological Conditions, Signs and Symptoms, Sensation Disorders, Signs and Symptoms, blindness (disorder), eye disorder, nervous system disorder, vision disorderNot yet recruitingNot applicable2024-04-12NCT06362434