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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Study to Evaluate the Efficacy and Safety of BMN 333 Versus Vosoritide in Children With AchondroplasiaBone Diseases, Developmental, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Dwarfism, achondroplasia, bone disorder, hereditary disease, musculoskeletal system disorder, osteochondrodysplasiaRecruitingPhase 2 / Phase 32026-09-24NCT07441876
Pediatricians Building Resilience Through Early Identification for Toddler Well-BeingMental HealthRecruitingNot applicable2026-07-08NCT07091240
Reduced Intensity Conditioning and Familial HLA-Mismatched BMT for Non-Malignant DisordersBone Marrow Failure Disorders, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, Nutritional and Metabolic Diseases, anemia, bone marrow disorder, familial hemolytic anemia, hematologic disorder, hemolytic anemia, hereditary disease, immune system disorder, inherited hemoglobinopathy, metabolic disease, sickle cell diseaseRecruitingPhase 1 / Phase 22026-05-29NCT03128996
A Socio-ecological Approach for Improving Self-management in Adolescents With SCDCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, anemia, familial hemolytic anemia, hematologic disorder, hemolytic anemia, hereditary disease, inherited hemoglobinopathy, sickle cell diseaseRecruitingNot applicable2026-05-11NCT06290401
Understanding the Long-term Impact of COVID on Children and FamiliesCOVID-19, Coronaviridae Infections, Infections, Nidovirales infectious disease, Orthocoronavirinae infectious disease, RNA Virus Infections, lung disorder, pneumonia, respiratory system disorder, respiratory tract infectious disorder, viral infectious disease, viral pneumoniaActive, not recruitingNot stated2025-12-31NCT05172011
Stress Hydrocortisone In Pediatric Septic ShockInfections, Inflammation, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Sepsis, Shock, Systemic Inflammatory Response Syndrome, toxic shock syndromeRecruitingPhase 32025-10-30NCT03401398
Optimal Ventilation for Cardiac Arrestcardiac arrest, cardiovascular disorder, heart disorderRecruitingNot applicable2025-10-08NCT07114510