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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
ATrial Tachycardia PAcing Therapy in Congenital HeartCardiovascular Abnormalities, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, atrial tachycardia, cardiovascular disorder, congenital heart disease, heart disorderRecruitingNot stated2026-03-13NCT03209583
A Long-Term Study of Bivamelagon in Participants With Hypothalamic Obesity (HO)Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Female Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Froelich syndrome, Male Urogenital Diseases, Urogenital Abnormalities, Urogenital Diseases, disorder of sexual differentiation, endocrine system disorder, gonadal disorder, gonadal dysgenesis, hypogonadismEnrolling by invitationPhase 22026-02-10NCT07156578
An Open-Label Extension Study of STK-001 for Patients With Dravet SyndromeEpilepsies, Myoclonic, Epilepsy, Generalized, Epileptic Syndromes, brain disorder, central nervous system disorder, epilepsy, nervous system disorderActive, not recruitingPhase 22026-02-04NCT04740476
Givinostat in Duchenne's Muscular Dystrophy Long-term Safety and Tolerability StudyCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne muscular dystrophy, Muscular Disorders, Atrophic, X-linked disease, hereditary disease, muscle tissue disorder, muscular dystrophy, musculoskeletal system disorder, nervous system disorder, neuromuscular diseaseRecruitingPhase 2 / Phase 32026-01-21NCT03373968
National Collaborative to Improve Care of Children With Complex Congenital Heart DiseaseCardiovascular Abnormalities, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, cardiovascular disorder, congenital heart disease, heart disorder, hypoplastic left heart syndromeRecruitingNot stated2025-06-19NCT02852031