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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Clinical Trial in Patients With Barth Syndrome- 4TAZPowerAbnormalities, Multiple, Barth syndrome, Cardiovascular Abnormalities, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Lipid Metabolism Disorders, Lipid Metabolism, Inborn Errors, Nutritional and Metabolic Diseases, X-linked disease, cardiovascular disorder, congenital heart disease, heart disorder, hereditary disease, inborn errors of metabolism, metabolic diseaseRecruitingPhase 42026-09-17NCT07531251