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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
A Study to Assess Growth in Children With Idiopathic Short StatureIdiopathic Short StatureRecruitingNot stated2026-06-23NCT06309979
An Extension Study to Evaluate Safety and Efficacy of BMN 111 in Children With AchondroplasiaBone Diseases, Developmental, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Dwarfism, achondroplasia, bone disorder, endocrine system disorder, hereditary disease, musculoskeletal system disorder, osteochondrodysplasiaActive, not recruitingPhase 22026-03-13NCT03989947
An Extension Study to Evaluate the Efficacy and Safety of BMN 111 in Children With AchondroplasiaBone Diseases, Developmental, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Dwarfism, achondroplasia, bone disorder, endocrine system disorder, hereditary disease, musculoskeletal system disorder, osteochondrodysplasiaActive, not recruitingPhase 32026-03-13NCT03424018
A Multicenter Multinational Observational Study of Children With HypochondroplasiahypochondroplasiaRecruitingNot stated2025-04-03NCT06212947