Hôpital Necker Enfants Malades
Hôpital Necker Enfants Malades
Paris, France18 results · Page 1 of 1
Clinical trials
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| Trial | Conditions | Status | Phase | Updated | More info | NCT ID |
|---|---|---|---|---|---|---|
| A Study to Provide Access to Mitapivat for Participants Who Previously Participated in an Agios-Sponsored Mitapivat Study | Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, anemia, familial hemolytic anemia, hematologic disorder, hemolytic anemia, hereditary disease, inherited hemoglobinopathy, pyruvate kinase deficiency of red cells, sickle cell disease, thalassemia | Enrolling by invitation | Phase 4 | 2026-09-29 | NCT05777993 | |
| Quality of Life Before and After Transcatheter Ablation in Children With Arrythmias | Arrhythmias, Cardiac, Pathologic Processes, Pathological Conditions, Signs and Symptoms, cardiovascular disorder, heart disorder | Recruiting | Not stated | 2026-09-28 | NCT06808204 | |
| A Study Evaluating the Efficacy and Safety of Mitapivat in Participants With Transfusion-Dependent Alpha- or Beta-Thalassemia (α- or β-TDT) | Transfusion-dependent Alpha-Thalassemia; Transfusion-dependent Beta-Thalassemia | Active, not recruiting | Phase 3 | 2026-09-28 | NCT04770779 | |
| Evaluation of Oral Tofacitinib in Children Aged 2 to 17 Years Old Suffering From Moderate to Severe Ulcerative Colitis | Digestive System Diseases, colitis, colonic disorder, digestive system disorder, gastroenteritis, inflammatory bowel disease, intestinal disorder, ulcerative colitis | Active, not recruiting | Phase 3 | 2026-08-03 | NCT04624230 | |
| Announcement of Rare Metabolic Diseases in Systematic Newborn Screening: the Phenylketonuria Experience. | Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Disease Attributes, Nutritional and Metabolic Diseases, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Psychological Trauma, Rare Diseases, Stress Disorders, Traumatic, acute stress disorder, brain disorder, central nervous system disorder, hereditary disease, inborn disorder of amino acid metabolism, inborn errors of metabolism, metabolic disease, nervous system disorder, phenylketonuria, psychiatric disorder | Recruiting | Not stated | 2026-06-24 | NCT06289348 | |
| Interactive Guidance Therapy With Video Feed-back of Parent and Child With Autism Spectrum Disorder | autism spectrum disorder, neurodevelopmental disorder, pervasive developmental disorder, psychiatric disorder | Active, not recruiting | Not applicable | 2026-05-06 | NCT04607616 | |
| High-throughput Omic Technology for Identification of Biomarkers of Relapsing Acute Disseminated Encephalomyelitis in Immune Cell Network | CNS demyelinating autoimmune disease, Chronic Disease, Disease Attributes, Leukoencephalopathies, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Post-Infectious Disorders, acute disseminated encephalomyelitis, autoimmune disease, autoimmune disorder of the nervous system, brain disorder, central nervous system disorder, demyelinating disease, immune system disorder, nervous system disorder | Recruiting | Not applicable | 2026-04-27 | NCT06863974 | |
| Clinico-biological Characterization and Survival of Patients With Adult T-cell Leukemia / Lymphoma (ATL) and Patients Chronically Infected With the HTLV-1 Virus (HTLV-OBS) | Hemic and Lymphatic Diseases, Infections, Neoplasms by Histologic Type, RNA Virus Infections, deltaretrovirus infections, hematologic disorder, human T-lymphotropic virus 1 infectious disease, immune system disorder, immunoproliferative disorder, inborn error of immunity, leukemia, lymphatic system disorder, lymphoma, lymphoproliferative syndrome, neoplasm, uterine carcinosarcoma, viral infectious disease | Active, not recruiting | Not stated | 2026-03-25 | NCT05237245 | |
| Respiratory and Psychological Impact of Elective Surgery of Congenital Lung Malformations | Congenital Lung Malformations | Recruiting | Not stated | 2026-03-23 | NCT06424392 | |
| Global Patient Registry to Monitor Long-term Safety and Effectiveness of Increlex® in Children and Adolescents With Severe Primary Insulin-like Growth Factor-1 Deficiency (SPIGFD). | growth delay due to insulin-like growth factor type 1 deficiency | Recruiting | Not stated | 2026-02-06 | NCT00903110 | |
| Letermovir-based Dual Therapy for Treatment of Cytomegalovirus Infections | DNA Virus Infections, Herpesviridae infectious disease, Infections, cytomegalovirus infection, viral infectious disease | Recruiting | Phase 3 | 2026-01-02 | NCT06334497 | |
| Understanding the Mechanisms of Autism : an MRI and Social Cognition Study | autism spectrum disorder, neurodevelopmental disorder, pervasive developmental disorder, psychiatric disorder | Recruiting | Not applicable | 2025-12-23 | NCT06334588 | |
| Characterization of Autoreactive Regulatory and Conventional CD4 T Cells in Recent Onset Type 1 Diabetes and Control Individuals | Nutritional and Metabolic Diseases, autoimmune disease, diabetes mellitus, endocrine system disorder, glucose metabolism disease, immune system disorder, metabolic disease, type 1 diabetes mellitus | Recruiting | Not applicable | 2025-11-20 | NCT06427421 | |
| Immunomonitoring of Mold Invasive Infections | Bacterial Infections and Mycoses, Infections, Invasive Fungal Infections, fungal infectious disease | Recruiting | Not stated | 2025-11-20 | NCT06285188 | |
| Interest of Preoperative Arteriography to Identify the Adamkiewicz Artery Before Surgery for Basi-thoracic Neuroblastic Tumors | Neoplasms by Histologic Type, Neoplasms, Germ Cell and Embryonal, Neoplasms, Nerve Tissue, Neuroectodermal Tumors, Primitive, Neuroectodermal Tumors, Primitive, Peripheral, epithelial neoplasm, ganglioneuroblastoma, neoplasm, neuroblastoma, neuroepithelial neoplasm, primitive neuroectodermal tumor | Not yet recruiting | Not stated | 2025-09-12 | NCT06798532 | |
| Safety and Efficacy Study of reSept ASD Occluder for Treating Secundum ASD | Cardiovascular Abnormalities, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, atrial septal defect, cardiovascular disorder, congenital heart disease, heart disorder, heart septal defect | Active, not recruiting | Not applicable | 2025-05-07 | NCT04591392 | |
| Understanding the Long-Term Management of Organic Acidemia Patients With CARBAGLU®: A Mixed Methods Approach | Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Nutritional and Metabolic Diseases, hereditary disease, inborn disorder of amino acid metabolism, inborn errors of metabolism, metabolic disease, methylmalonic acidemia, propionic acidemia | Recruiting | Not stated | 2024-02-05 | NCT04176523 | |
| Juvenile Recurrent Respiratory Papillomatosis: Establishment of a French National Cohort (PRR : National Cohort " REPA ") | Juvenile Recurrent Respiratory Papillomatosis | Recruiting | Not stated | 2023-08-21 | NCT06000527 |