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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Clinical, Electrophysiological and Genetic Characteristics of Hereditary and Inflammatory Polyneuropathies in FranceCharcot-Marie-Tooth disease, Chronic Disease, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Disease Attributes, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Rare Diseases, autoimmune disease, autoimmune disorder of the nervous system, central nervous system malformation, chronic inflammatory demyelinating polyradiculoneuropathy, demyelinating disease, hereditary disease, hereditary motor and sensory neuropathy, immune system disorder, inherited neurodegenerative disorder, nervous system disorder, neuritis, neurodegenerative disease, neuromuscular disease, peripheral nervous system disorder, polyneuropathy, polyradiculoneuropathyNot yet recruitingNot stated2026-10-01NCT07851844
Pharmacokinetics, Efficacy and Safety of Twice Daily Dosing Regimen of Hydroxycarbamide Dispersible Tablets in Children With Sickle Cell DiseaseCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, anemia, familial hemolytic anemia, hematologic disorder, hemolytic anemia, hereditary disease, inherited hemoglobinopathy, sickle cell diseaseRecruitingPhase 22026-10-01NCT06578507
Efficacy and Safety of BUFY02 Versus TRB02 in the Treatment of Dry Eye Diseasedry eye syndrome, eye disorder, lacrimal apparatus disorderRecruitingNot applicable2026-09-29NCT05865457
Effect of Adding Vasopressin on Cardiac Output, Blood Pressure, Diuresis, and Tissue Perfusion Indices in Patients With Septic ShockFemale Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Infections, Inflammation, Male Urogenital Diseases, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Sepsis, Shock, Systemic Inflammatory Response Syndrome, Urogenital Diseases, diabetes insipidus, endocrine system disorder, kidney disorder, pituitary gland disorder, toxic shock syndrome, urinary system disorderNot yet recruitingNot stated2026-07-13NCT07697144
Assessment of the Reproducibility of the Recruitment-to-inflation Ratio (R/I Ratio) Measurement in Patients With Acute Respiratory Distress SyndromeRespiration Disorders, adult acute respiratory distress syndrome, lung disorder, respiratory system disorderNot yet recruitingNot stated2026-06-24NCT07666503
Epidemiology of Invasive Bacterial Infections in Children With Sickle Cell Disease in France Between 2020 and 2025Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, anemia, familial hemolytic anemia, hematologic disorder, hemolytic anemia, hereditary disease, inherited hemoglobinopathy, sickle cell diseaseNot yet recruitingNot stated2026-06-10NCT07639008
Comparison of Weekly Somatrogon to Daily Genotropin in Children Born Small for Gestational Age or With Idiopathic Short Stature.ISS; SGARecruitingPhase 32026-04-30NCT07226089
Efficacy and Safety of Obefazimod in Subjects With Moderately to Severely Active Crohn's DiseaseCrohn disease, Digestive System Diseases, digestive system disorder, gastroenteritis, inflammatory bowel disease, intestinal disorderRecruitingPhase 22026-04-27NCT06456593
Factors Associated With Blood Pressure Control Failure to Intravenous Labetalol in Severe PreeclampsiaFemale Urogenital Diseases and Pregnancy Complications, Urogenital Diseases, hypertension, pregnancy-induced, preeclampsia, pregnancy disorder, severe pre-eclampsiaNot yet recruitingNot stated2026-04-23NCT07547046
Randomized Controlled Multicenter Study Comparing Steroid Therapy Plus Anticoagulants to Steroid Therapy Alone in Deep Venous Thrombosis of Behçet's SyndromeBehcet disease, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Skin and Connective Tissue Diseases, Stomatognathic Diseases, anterior uveitis, cardiovascular disorder, eye disorder, hereditary disease, hereditary periodic fever syndrome, hereditary skin disorder, mouth disorder, panuveitis, skin disorder, skin vascular disease, uveal disorder, uveitis, vascular disorder, vasculitisRecruitingPhase 32026-04-23NCT06780462
DCP (RaDiCo Cohort) (RaDiCo-DCP)Abnormalities, Multiple, Ciliopathies, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, hereditary disease, otorhinolaryngologic disease, primary ciliary dyskinesia, respiratory system disorderRecruitingNot stated2026-02-12NCT05951478
IDMet (RaDiCo Cohort) (RaDiCo-IDMet)Abnormalities, Multiple, Angelman syndrome, Beckwith-Wiedemann syndrome, Bone Diseases, Metabolic, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Craniofacial Abnormalities, Dwarfism, Imprinting Disorders, Musculoskeletal Abnormalities, Neurobehavioral Manifestations, Neurologic Manifestations, Nutritional and Metabolic Diseases, Overweight, Prader-Willi syndrome, Silver-Russell syndrome, Temple syndrome, bone disorder, calcium metabolic disease, central nervous system disorder, chromosomal disorder, endocrine system disorder, gonadal disorder, hereditary disease, inborn errors of metabolism, inborn metal metabolism disorder, intellectual disability, metabolic disease, movement disorder, multiple congenital anomalies due to 14q32.2 maternally expressed gene defect, musculoskeletal system disorder, nervous system disorder, nutritional disorder, obesity disorder, overnutrition, paternal uniparental disomy of chromosome 14, precocious puberty, pseudohypoparathyroidism, transient neonatal diabetes mellitusRecruitingNot stated2026-02-12NCT05945576
French eCLIPs™ Efficacy and Safety InvestigationAneurysm, brain aneurysm, brain disorder, cardiovascular disorder, central nervous system disorder, cerebrovascular disorder, intracranial arterial disease, nervous system disorder, vascular disorderActive, not recruitingNot applicable2025-08-15NCT05330897
Hizentra® in Inflammatory Neuropathies - pHeNIx StudyChronic Disease, Disease Attributes, Pathologic Processes, Pathological Conditions, Signs and Symptoms, autoimmune disease, autoimmune disorder of the nervous system, chronic inflammatory demyelinating polyradiculoneuropathy, demyelinating disease, immune system disorder, nervous system disorder, neuromuscular disease, peripheral nervous system disorder, polyneuropathy, polyradiculoneuropathyRecruitingNot stated2025-01-07NCT04672733
Pediatric -Adult Care Transition Program of Patients With Sickle Cell DiseaseCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, anemia, familial hemolytic anemia, hematologic disorder, hemolytic anemia, hereditary disease, inherited hemoglobinopathy, sickle cell diseaseRecruitingNot applicable2024-06-21NCT03786549