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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
HCRN Endoscopic Versus Shunt Treatment of Hydrocephalus in Infantsbrain disorder, central nervous system disorder, hydrocephalus, nervous system disorderActive, not recruitingNot applicable2026-09-25NCT04177914
ZIP Study-OL Study of Safety, PK, Efficacy, PD, Immunogenicity of ATB200/AT2221 in Pediatrics Aged 0 to < 18 y.o. w/LOPDBrain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Lysosomal Storage Diseases, Nervous System, Nutritional and Metabolic Diseases, brain disorder, central nervous system disorder, disorder of glycogen metabolism, glycogen storage disease II, hereditary disease, inborn carbohydrate metabolic disorder, inborn errors of metabolism, lysosomal storage disease, metabolic disease, nervous system disorderActive, not recruitingPhase 32026-09-17NCT03911505
Multisite Inventory of Neonatal-Perinatal Interventions (MINI) Minimum DatasetFemale Urogenital Diseases and Pregnancy Complications, Obstetric Labor Complications, Obstetric Labor, Premature, Premature Birth, Urogenital Diseases, pregnancy disorderRecruitingNot stated2026-07-06NCT05685745
A Global Prospective Observational Registry of Patients With Pompe DiseaseBrain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Lysosomal Storage Diseases, Nervous System, Nutritional and Metabolic Diseases, brain disorder, central nervous system disorder, disorder of glycogen metabolism, glycogen storage disease II, hereditary disease, inborn carbohydrate metabolic disorder, inborn errors of metabolism, lysosomal storage disease, metabolic disease, nervous system disorderRecruitingNot stated2026-03-10NCT06121011
Post-approval Registry Study to Evaluate the Continued Safety and Probable Benefit of the MID-C System for 5 Years Post-Implantation in Adolescent Idiopathic Scoliosis (AIS)adolescent idiopathic scoliosisActive, not recruitingNot applicable2025-10-03NCT04296903
IBP-9414 for the Prevention of Necrotizing Enterocolitis - The Connection StudyDigestive System Diseases, digestive system disorder, enterocolitis, gastroenteritis, intestinal disorder, necrotizing enterocolitisActive, not recruitingPhase 32024-04-12NCT03978000