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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Campath/Fludarabine/Melphalan Transplant Conditioning for Non-Malignant DiseasesCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, Nutritional and Metabolic Diseases, hematologic disorder, hereditary disease, inherited hemoglobinopathy, metabolic diseaseRecruitingPhase 1 / Phase 22026-09-16NCT00920972
CNP-103 in Adolescent and Adult Subjects Ages 12-35 With Recently Diagnosed (Within 6 Months) Stage 3 Type 1 Diabetes (T1D)Nutritional and Metabolic Diseases, autoimmune disease, diabetes mellitus, endocrine system disorder, glucose metabolism disease, immune system disorder, metabolic disease, type 1 diabetes mellitusRecruitingPhase 1 / Phase 22026-09-11NCT06783309
Remedy to Diabetes Distress (R2D2): A Scalable Screen to Treat Program for School-age FamiliesNutritional and Metabolic Diseases, autoimmune disease, diabetes mellitus, endocrine system disorder, glucose metabolism disease, immune system disorder, metabolic disease, type 1 diabetes mellitusRecruitingNot applicable2026-09-01NCT05268250
A Double-blind Study Evaluating the Efficacy, Safety, and Tolerability of Zorevunersen in Patients With Dravet SyndromeEpilepsies, Myoclonic, Epilepsy, Generalized, Epileptic Syndromes, brain disorder, central nervous system disorder, epilepsy, nervous system disorderRecruitingPhase 32026-08-24NCT06872125
A Study of Dulaglutide (LY2189265) 3.0 mg and 4.5 mg in Pediatric Participants With Type 2 Diabetes Mellitus (AWARD-PEDS PLUS)Nutritional and Metabolic Diseases, diabetes mellitus, endocrine system disorder, glucose metabolism disease, metabolic disease, type 2 diabetes mellitusRecruitingPhase 32026-08-07NCT06739122
Breaking Disparities in Access to Advanced Diabetes Technologies in Children With Type 1 DiabetesNutritional and Metabolic Diseases, autoimmune disease, diabetes mellitus, endocrine system disorder, glucose metabolism disease, immune system disorder, metabolic disease, type 1 diabetes mellitusRecruitingNot stated2026-07-20NCT05849753
Pharmacokinetics, Efficacy, and Safety of Encaleret in Pediatric Participants With Autosomal Dominant Hypocalcemia Type 1 (ADH1)Autosomal Dominant Hypocalcemia Type 1 (ADH1)RecruitingPhase 2 / Phase 32026-04-22NCT07080385
Optimizing a Sensor-Enabled mHealth Intervention for Adolescents With Suboptimal Asthma ControlHypersensitivity, Immediate, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Respiratory Hypersensitivity, asthma, bronchial disorder, disease, immune system disorder, lung disorder, obstructive lung disease, respiratory system disorderRecruitingNot applicable2025-12-24NCT07301060
The Tether™ - Vertebral Body Tethering System Post Approval StudyScoliosis IdiopathicRecruitingNot stated2024-02-22NCT04505579