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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
A Study Evaluating the Long-term Safety and Efficacy of VX-121 Combination TherapyCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, Infant, Newborn, Diseases, cystic fibrosis, hereditary disease, lung disorder, pancreas disorder, respiratory system disorderActive, not recruitingPhase 32026-10-09NCT05444257
A Non-interventional Study of Participants With BPDCN Treated With ChemotherapyCD4+/CD56+ hematodermic neoplasm, Hemic and Lymphatic Diseases, Neoplasms by Histologic Type, Neoplasms by Site, Skin and Connective Tissue Diseases, hematologic disorder, hematopoietic and lymphoid system neoplasm, leukemia, lymphoma, malignant histiocytosis, neoplasm, skin disorder, skin neoplasmRecruitingNot stated2026-09-15NCT07785180
A Safety and Efficacy Study of GTX-102 in Subjects With Deletion- or Nondeletion-type Angelman Syndrome (AS)Abnormalities, Multiple, Angelman syndrome, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Imprinting Disorders, central nervous system disorder, chromosomal disorder, hereditary disease, movement disorder, nervous system disorderActive, not recruitingPhase 22026-09-09NCT07157254
Xeltis Hemodialysis Access (aXess) Conduit: aXess-E StudyChronic Disease, Disease Attributes, Female Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Male Urogenital Diseases, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Urogenital Diseases, chronic renal failure syndrome, kidney disorder, kidney failure, urinary system disorderRecruitingNot applicable2026-07-29NCT06329310
Observation of Clinical Routine Care for Heart Failure Patients Implanted With BIOTRONIK CRT Devicescardiovascular disorder, heart disorder, heart failureActive, not recruitingNot stated2026-02-12NCT03366545
Efficacy and Safety of Masitinib Versus Placebo in the Treatment of ALS PatientsNutritional and Metabolic Diseases, TDP-43 proteinopathy, amyotrophic lateral sclerosis, central nervous system disorder, metabolic disease, motor neuron disorder, nervous system disorder, neurodegenerative disease, neuromuscular disease, proteostasis deficiencies, spinal cord disorderRecruitingPhase 32025-09-12NCT03127267
The European NAFLD RegistryBody Weight, Digestive System Diseases, Digestive System Neoplasms, Dyslipidemias, Fibrosis, Fibrosis, Liver, Lipid Metabolism Disorders, Liver Neoplasms, Neoplasms by Histologic Type, Neoplasms by Site, Nutritional and Metabolic Diseases, Overweight, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Signs and Symptoms, Steatohepatitis, adenocarcinoma, carcinoma, cardiovascular disorder, cirrhosis of liver, diabetes mellitus, endocrine system disorder, epithelial neoplasm, fatty liver disease, glucose metabolism disease, hepatocellular carcinoma, hypertensive disorder, liver disorder, metabolic disease, metabolic dysfunction-associated steatohepatitis, metabolic dysfunction-associated steatotic liver disease, neoplasm, nutritional disorder, obesity disorder, overnutrition, type 2 diabetes mellitus, vascular disorderRecruitingNot stated2023-01-06NCT04442334