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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Trial of Therapeutic Cancer Vaccine OSE2101 in Patients With Non-Small Cell Lung Cancer and Secondary Resistance to Immune Checkpoint InhibitorNeoplasms by Site, Thoracic Neoplasms, bronchial neoplasm, bronchogenic carcinoma, lung disorder, lung neoplasm, neoplasm, non-small cell lung carcinoma, respiratory system disorder, respiratory tract neoplasmRecruitingPhase 32026-10-02NCT06472245
A Study of Mosliciguat in PH-ILDFibrosis, Pathologic Processes, Pathological Conditions, Signs and Symptoms, cardiovascular disorder, hypertensive disorder, interstitial lung disease, lung disorder, pulmonary hypertension, respiratory system disorder, vascular disorderActive, not recruitingPhase 22026-09-10NCT06635850
Study to Evaluate Efficacy and Safety of Firmonertinib Compared With Investigator's Choice of EGFR Inhibitor as First-Line Treatment in Participants Who Have Locally Advanced or Metastatic NSCLC With EGFR P-Loop and Alpha C-Helix Compressing (PACC) Uncommon MutationsNeoplasms by Site, Thoracic Neoplasms, bronchial disorder, bronchial neoplasm, bronchogenic carcinoma, lung disorder, lung neoplasm, neoplasm, non-small cell lung carcinoma, respiratory system disorder, respiratory tract neoplasmRecruitingPhase 32026-09-01NCT07185997
A Study to Assess Zipalertinib Versus Placebo in Participants With Early Stage NSCLC With Uncommon EGFR Mutations, Following Complete Tumor ResectionNeoplasms by Site, Thoracic Neoplasms, bronchial neoplasm, bronchogenic carcinoma, lung cancer, lung disorder, lung neoplasm, neoplasm, non-small cell lung carcinoma, respiratory system disorder, respiratory tract neoplasmActive, not recruitingPhase 32026-08-26NCT07128199
Clinical Trial of Inhaled Molgramostim Nebulizer Solution in Autoimmune Pulmonary Alveolar Proteinosis (aPAP)autoimmune pulmonary alveolar proteinosisActive, not recruitingPhase 32026-08-26NCT04544293
A Study of How the Medicine Called "Etrasimod" Works in Children With the Gut Disease Called Ulcerative ColitisDigestive System Diseases, Pathologic Processes, Pathological Conditions, Signs and Symptoms, colitis, colonic disorder, digestive system disorder, gastroenteritis, inflammatory bowel disease, intestinal disorder, ulcer disease, ulcerative colitisRecruitingPhase 22026-08-24NCT07470879
A Trial of Lu AG13909 in Adult Participants With Cushing's DiseaseACTH-dependent Cushing syndrome, brain disorder, central nervous system disorder, endocrine system disorder, hyperpituitarism, hypothalamic disorder, nervous system disorder, pituitary gland disorderRecruitingPhase 22026-08-21NCT06471829
A Study of Ixekizumab (LY2439821) in Children With Juvenile Idiopathic Arthritis Categories of Enthesitis-related Arthritis (Including Juvenile Onset Ankylosing Spondylitis) and Juvenile Psoriatic ArthritisSkin and Connective Tissue Diseases, arthritic joint disease, arthropathy, autoimmune disease, connective tissue disorder, immune system disorder, juvenile idiopathic arthritis, musculoskeletal system disorder, rheumatic disorderActive, not recruitingPhase 32026-08-12NCT04527380
International Wilson's Disease Patient Registry (iWilson Registry)Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, Nutritional and Metabolic Diseases, Wilson disease, basal ganglia disorder, brain disorder, central nervous system disorder, hereditary disease, inborn errors of metabolism, inborn metal metabolism disorder, inherited neurodegenerative disorder, liver disorder, metabolic disease, movement disorder, nervous system disorder, neurodegenerative diseaseRecruitingNot stated2026-08-11NCT05239858
Study of RAS(ON) Inhibitors in Patients With Advanced RAS-mutated NSCLCNeoplasms by Site, Thoracic Neoplasms, bronchial neoplasm, bronchogenic carcinoma, lung disorder, lung neoplasm, neoplasm, non-small cell lung carcinoma, respiratory system disorder, respiratory tract neoplasmRecruitingPhase 1 / Phase 22026-06-30NCT06162221
Long-Term Low-Intervention SafEty and Clinical Outcomes Clinical Study of LivmArli® in Patients With Alagille Syndrome or Progressive Familial Intrahepatic Cholestasis in the European Union (LEAP-EU)Abnormalities, Multiple, Alagille syndrome, Cardiovascular Abnormalities, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, Pathological Conditions, Signs and Symptoms, Pruritus, Signs and Symptoms, Skin Manifestations, Skin and Connective Tissue Diseases, bile duct disorder, biliary tract disorder, cardiovascular disorder, cholestasis, congenital heart disease, hereditary disease, intrahepatic cholestasis, liver disorder, progressive familial intrahepatic cholestasis type 1, skin disorderRecruitingPhase 42026-06-23NCT07290257
Bright Light Therapy During Inpatient Cocaine DetoxificationChemically-Induced Disorders, Cocaine-Related Disorders, psychiatric disorder, substance-related disorderRecruitingNot applicable2026-06-12NCT07545798
Impact of Cocaine Use and Withdrawal on SleepCocaine Use DisorderRecruitingNot stated2026-06-11NCT07119567
ADH1 and ADH2 Disease Monitoring Study (DMS)Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Female Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Hypercalciuria, Hypercalciuric Hypocalcemia, Familial, Hypocalcemia, Male Urogenital Diseases, Musculoskeletal Abnormalities, Nutritional and Metabolic Diseases, Pathological Conditions, Signs and Symptoms, Signs and Symptoms, Urogenital Diseases, Urological Manifestations, Water-Electrolyte Imbalance, autosomal dominant hypocalcemia, calcinosis, calcium metabolic disease, endocrine system disorder, hypoparathyroidism, kidney disorder, metabolic disease, muscle tissue disorder, musculoskeletal system disorder, nephrocalcinosis, nephrolithiasis, nervous system disorder, neuromuscular disease, parathyroid gland disorder, urinary system disorder, urolithiasisActive, not recruitingNot stated2026-04-30NCT05227287
A Study to Evaluate the Efficacy, Safety, and Tolerability of BMS-986278 in Participants With Progressive Pulmonary FibrosisFibrosis, Hemic and Lymphatic Diseases, Hypersensitivity, Delayed, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Skin and Connective Tissue Diseases, arthritic joint disease, arthropathy, autoimmune disease, connective tissue disorder, diffuse scleroderma, immune system disorder, interstitial lung disease, lung disorder, lymphatic system disorder, lymphoproliferative syndrome, musculoskeletal system disorder, pulmonary fibrosis, respiratory system disorder, rheumatic disorder, rheumatoid arthritis, sarcoidosis, skin disorder, systemic sclerosisActive, not recruitingPhase 32026-04-23NCT06025578
To Evaluate the Efficacy of CVN424 in Parkinson's Disease Participants With Motor ComplicationsParkinson disease, basal ganglia disorder, brain disorder, central nervous system disorder, movement disorder, nervous system disorder, neurodegenerative disease, parkinsonian disorder, synucleinopathyActive, not recruitingPhase 32026-04-17NCT06553027
A Study to Evaluate the Efficacy, Safety, and Tolerability of BMS-986278 in Participants With Idiopathic Pulmonary FibrosisFibrosis, Pathologic Processes, Pathological Conditions, Signs and Symptoms, idiopathic pulmonary fibrosis, interstitial lung disease, lung disorder, pulmonary fibrosis, respiratory system disorderActive, not recruitingPhase 32026-03-24NCT06003426
Lysosomal Acid Lipase (LAL) Deficiency RegistryAcid Cholesteryl Ester Hydrolase Deficiency, Type 2, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Infant, Newborn, Diseases, Lipid Metabolism Disorders, Lipid Metabolism, Inborn Errors, Nutritional and Metabolic Diseases, Wolman disease, cholesteryl ester storage disease, hereditary disease, inborn errors of metabolism, lysosomal lipid storage disorder, lysosomal storage disease, metabolic diseaseRecruitingNot stated2026-03-06NCT01633489
Modifying Factors in Striated Muscle LaminopathiesAutosomal Emery-Dreifuss Muscular Dystrophy, Cardiomegaly, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Emery-Dreifuss muscular dystrophy, Muscular Disorders, Atrophic, autosomal dominant Emery-Dreifuss muscular dystrophy, cardiomyopathy, cardiovascular disorder, congenital muscular dystrophy due to LMNA mutation, dilated cardiomyopathy, heart disorder, hereditary disease, laminopathy, muscle tissue disorder, muscular dystrophy, musculoskeletal system disorder, nervous system disorder, neuromuscular diseaseRecruitingNot applicable2026-03-04NCT05394506
Developmental Coordination Disorderdevelopmental coordination disorder, neurodevelopmental disorder, psychiatric disorderRecruitingNot applicable2026-01-16NCT05154799
High Dose Steroids in Children With StrokePathologic Processes, Pathological Conditions, Signs and Symptoms, brain disorder, cardiovascular disorder, central nervous system disorder, cerebrovascular disorder, ischemic disease, nervous system disorder, stroke disorder, vascular disorderRecruitingPhase 32025-11-18NCT04873583
Extension Study of Idursulfase-IT Along With Elaprase in Children and Adults With Hunter Syndrome and Cognitive ImpairmentCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Neurobehavioral Manifestations, Neurologic Manifestations, Nutritional and Metabolic Diseases, Skin and Connective Tissue Diseases, X-linked disease, connective tissue disorder, cutaneous mucinosis, hereditary disease, inborn carbohydrate metabolic disorder, inborn errors of metabolism, inherited neurodegenerative disorder, intellectual disability, lysosomal storage disease, metabolic disease, mucopolysaccharidosis, mucopolysaccharidosis type 2, nervous system disorderActive, not recruitingPhase 2 / Phase 32025-11-06NCT06031259
Source Monitoring Déficit in Neuropsychiatric PopulationBipolar and Related Disorders, bipolar disorder, mood disorder, psychiatric disorderRecruitingNot applicable2025-07-31NCT03886584
Trajectories and Reactions of Users and Relatives Consulting French Youth Addiction ServicesAddictionRecruitingNot stated2025-07-30NCT05609474