Long-Term Low-Intervention SafEty and Clinical Outcomes Clinical Study of LivmArli® in Patients With Alagille Syndrome or Progressive Familial Intrahepatic Cholestasis in the European Union (LEAP-EU)
Long-Term Low-Intervention SafEty and Clinical Outcomes Clinical Study of LivmArli® in Patients With Alagille Syndrome or Progressive Familial Intrahepatic Cholestasis in the European Union (LEAP-EU)
Recruiting · NCT07290257 · Registry updated 2026-06-23Clinical trials
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| Trial | Conditions | Status | Phase | Updated | More info | NCT ID |
|---|---|---|---|---|---|---|
| Long-Term Low-Intervention SafEty and Clinical Outcomes Clinical Study of LivmArli® in Patients With Alagille Syndrome or Progressive Familial Intrahepatic Cholestasis in the European Union (LEAP-EU) | Abnormalities, Multiple, Alagille syndrome, Cardiovascular Abnormalities, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, Pathological Conditions, Signs and Symptoms, Pruritus, Signs and Symptoms, Skin Manifestations, Skin and Connective Tissue Diseases, bile duct disorder, biliary tract disorder, cardiovascular disorder, cholestasis, congenital heart disease, hereditary disease, intrahepatic cholestasis, liver disorder, progressive familial intrahepatic cholestasis type 1, skin disorder | Recruiting | Phase 4 | 2026-06-23 | NCT07290257 |
1 results · Page 1 of 1
Organizations
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| Organizations | Linked trials |
|---|---|
| Mirum Pharmaceuticals, Inc. | 15 |
15 results · Page 1 of 1
Research sites
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| Research sites | City | Country | Linked trials |
|---|---|---|---|
| 2nd Paediatric Clinic P &A Kyriakou Children's Hospital | Athens | Greece | 1 |
| AO Ospedale PAPA GIOVANNI XXIII | Bergamo | Italy | 1 |
| Bicetre University Hospital | Le Kremlin-Bicêtre | France | 1 |
| Charite Berlin | Berlin | Germany | 1 |
| Children's University Hospital Essen | Essen | Germany | 1 |
| CHU de Toulouse - Hôpital des Enfants | Toulouse | France | 1 |
| Cliniques Universitaires Saint Luc (UCLouvain) | Brussels | Belgium | 1 |
| Hospices Civils de Lyon - Hopital Femme Mère Enfant | Bron | France | 1 |
| Hospital Universitairo Vall D'Hebron | Barcelona | Spain | 1 |
| Hospital Universitario La Paz | Madrid | Spain | 217 |
| Istituto mediterraneo trapianti - ISMETT | Palermo | Italy | 1 |
| Unidade Local de Saude de Coimbra Paediatric Department Avenida Afonso Romăo | Coimbra | Portugal | 1 |
| University Hospital Gent (UZ Gent) | Ghent | Belgium | 1 |
| University Hospital Hamburg-Eppendorf | Hamburg | Germany | 4 |
| University Medical Center Groningen (UMCG) | Groningen | Netherlands | 2 |