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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Study Assessing the Efficacy, Safety and PK of Alpelisib (BYL719) in Pediatric and Adult Patients With PIK3CA-related Overgrowth SpectrumPIK3CA-related Overgrowth Spectrum (PROS)Active, not recruitingPhase 22026-10-07NCT04589650
Safety and Efficacy of Fingolimod in Pediatric Patients With Multiple SclerosisBody Weight, CNS demyelinating autoimmune disease, Pathological Conditions, Signs and Symptoms, Signs and Symptoms, Thinness, autoimmune disease, autoimmune disorder of the nervous system, demyelinating disease, immune system disorder, multiple sclerosis, nervous system disorderActive, not recruitingPhase 32026-08-10NCT01892722
Study to Evaluate Efficacy and Safety of Inclisiran in Children With Heterozygous Familial HypercholesterolemiaCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Dyslipidemias, Hypercholesterolemia, Lipid Metabolism Disorders, Lipid Metabolism, Inborn Errors, Nutritional and Metabolic Diseases, Ventricular Outflow Obstruction, aortic valve disorder, aortic valve stenosis, cardiovascular disorder, familial hypercholesterolemia, heart disorder, heart failure, heart valve disorder, hereditary disease, hyperlipidemia, hyperlipoproteinemia, inborn errors of metabolism, metabolic diseaseRecruitingPhase 32026-05-15NCT06597019