Study to Evaluate Efficacy and Safety of Inclisiran in Children With Heterozygous Familial Hypercholesterolemia
Study to Evaluate Efficacy and Safety of Inclisiran in Children With Heterozygous Familial Hypercholesterolemia
Recruiting · NCT06597019 · Registry updated 2026-05-15Clinical trials
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| Trial | Conditions | Status | Phase | Updated | More info | NCT ID |
|---|---|---|---|---|---|---|
| Study to Evaluate Efficacy and Safety of Inclisiran in Children With Heterozygous Familial Hypercholesterolemia | Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Dyslipidemias, Hypercholesterolemia, Lipid Metabolism Disorders, Lipid Metabolism, Inborn Errors, Nutritional and Metabolic Diseases, Ventricular Outflow Obstruction, aortic valve disorder, aortic valve stenosis, cardiovascular disorder, familial hypercholesterolemia, heart disorder, heart failure, heart valve disorder, hereditary disease, hyperlipidemia, hyperlipoproteinemia, inborn errors of metabolism, metabolic disease | Recruiting | Phase 3 | 2026-05-15 | NCT06597019 |
1 results · Page 1 of 1
Organizations
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| Organizations | Linked trials |
|---|---|
| Novartis Pharmaceuticals | 432 |
9 results · Page 1 of 1
Research sites
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| Research sites | City | Country | Linked trials |
|---|---|---|---|
| Children's National Hospital | Washington D.C. | United States | 100 |
| Childrens National Hospital | Washington D.C. | United States | 10 |
| Excel Medical Clinical Trials LLC | Boca Raton | United States | 9 |
| Icahn School of Med at Mt Sinai | New York | United States | 6 |
| Primary Childrens Medical Center | Salt Lake City | United States | 3 |
| UC San Francisco Medical Center | San Francisco | United States | 3 |
| UC San Francisco Medical Center | San Francisco | United States | 2 |
| Virginia Commonwealth University | Richmond | United States | 156 |
| West Virginia Childrens Hospital | Morgantown | United States | 1 |