9 results ยท Page 1 of 1

Swipe the table sideways for more columns.

TrialConditionsStatusPhaseUpdatedMore infoNCT ID
The HOPE Biobank Resource (BMT CTN 2402 HOPE)Bone Marrow Failure, Bone Marrow Failure Disorders, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, anemia, aplastic anemia, bone marrow disorder, hematologic disorder, hereditary disease, inherited hemoglobinopathyRecruitingNot stated2026-08-27NCT07227155
Naive T Cell Deplete Grafts for GVHD Prevention in Non-Malignant DiseasesBone Marrow Failure, Bone Marrow Failure Disorders, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, Lymphohistiocytosis, Hemophagocytic, Primary Immunodeficiency Diseases, bone marrow disorder, hematologic disorder, hereditary disease, histiocytosis, immune system disorder, inborn error of immunity, inherited hemoglobinopathy, lymphatic system disorder, non-Langerhans cell histiocytosisNot yet recruitingPhase 22026-06-22NCT07660783
Cytokine-Treated Veto Cells in Treating Patients With Hematologic Malignancies Following Stem Cell TransplantB-cell chronic lymphocytic leukemia, Blood Protein Disorders, Bone Marrow Failure, Bone Marrow Failure Disorders, Chronic Disease, Disease Attributes, Hemic and Lymphatic Diseases, Hodgkins lymphoma, Leukemia, B-Cell, Leukemia, Myelogenous, Chronic, BCR-ABL Positive, Myeloproliferative Disorders, Neoplasms by Histologic Type, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Precursor Cell Lymphoblastic Leukemia-Lymphoma, acute myeloid leukemia, anemia, aplastic anemia, bone marrow disorder, cardiovascular disorder, chronic myeloid leukemia, follicular lymphoma, hematologic disorder, hemorrhagic disease, immune system disorder, immunoproliferative disorder, leukemia, lymphatic system disorder, lymphoid leukemia, lymphoma, lymphoproliferative syndrome, mantle cell lymphoma, monoclonal gammopathy, myelodysplastic syndrome, myeloid leukemia, myeloproliferative neoplasm, neoplasm, non-Hodgkin lymphoma, plasma cell myeloma, plasma cell neoplasm, vascular disorder, vascular hemostatic diseaseActive, not recruitingPhase 1 / Phase 22026-06-11NCT03622788
Phase 1/2: CD45RA Depleted Stem Cell Addback to Prevent Viral or Fungal Infections Post TCRab/CD19 Depleted HSCTBone Marrow Failure, Bone Marrow Failure Disorders, Congenital Bone Marrow Failure Syndromes, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, Infant, Newborn, Diseases, Neoplasms by Histologic Type, Nutritional and Metabolic Diseases, acquired aplastic anemia, anemia, bone marrow disorder, hematologic disorder, hemophagocytic syndrome, hereditary disease, immune system disorder, immunodeficiency disease, immunoproliferative disorder, inborn error of immunity, inborn errors of metabolism, inherited hemoglobinopathy, leukemia, lymphatic system disorder, lymphoma, lymphoproliferative syndrome, metabolic disease, myelodysplastic syndrome, myelodysplastic syndrome with excess blasts, myelodysplastic syndrome with single lineage dysplasia, neoplasmRecruitingPhase 1 / Phase 22026-04-15NCT06839456
Cord Blood Transplant in Children and Young Adults With Blood Cancers and Non-malignant DisordersBone Marrow Failure, Bone Marrow Failure Disorders, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, Myeloproliferative Disorders, Neoplasms by Histologic Type, acute lymphoblastic leukemia, acute myeloid leukemia, anemia, bone marrow disorder, hematologic disorder, hemophagocytic syndrome, hereditary disease, immune system disorder, immunoproliferative disorder, inherited hemoglobinopathy, leukemia, lymphatic system disorder, lymphoma, lymphoproliferative syndrome, myelodysplastic syndrome, myelodysplastic syndrome with excess blasts, myelodysplastic syndrome with single lineage dysplasia, myeloid leukemia, neoplasmRecruitingPhase 22026-03-13NCT04644016
Study to Evaluate of EXG34217 in Patients With Telomere Biology Disorders With Bone Marrow FailureBone Marrow Failure, Bone Marrow Failure Disorders, Hemic and Lymphatic Diseases, bone marrow disorder, hematologic disorderActive, not recruitingPhase 12026-02-06NCT04211714
Alpha/Beta TCD HCT in Patients With Inherited BMF DisordersBone Marrow Failure, Bone Marrow Failure Disorders, Congenital Abnormalities, Congenital Bone Marrow Failure Syndromes, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, DNA repair disease, Fanconi anemia, Hemic and Lymphatic Diseases, Nutritional and Metabolic Diseases, Skin Abnormalities, Skin and Connective Tissue Diseases, X-linked disease, anemia, aplastic anemia, bone marrow disorder, dyskeratosis congenita, hematologic disorder, hereditary disease, hereditary skin disorder, inherited aplastic anemia, metabolic disease, myelodysplastic syndrome, skin disorderRecruitingPhase 22026-01-30NCT03579875
Regenerative Medicine to Restore Hematopoiesis and Immune Function in Immunodeficiencies and Inherited Bone Marrow FailuresBone Marrow Failure, Bone Marrow Failure Disorders, Congenital Abnormalities, Congenital Bone Marrow Failure Syndromes, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, DNA repair disease, Fanconi anemia, Hemic and Lymphatic Diseases, Hoyeraal-Hreidarsson syndrome, Immune Deficiency Disease, Nutritional and Metabolic Diseases, Primary Immunodeficiency Diseases, Skin Abnormalities, Skin and Connective Tissue Diseases, X-linked disease, anemia, aplastic anemia, bone marrow disorder, dyskeratosis congenita, hematologic disorder, hereditary disease, hereditary skin disorder, immune system disorder, inborn error of immunity, inherited aplastic anemia, metabolic disease, skin disorder, telomere syndromeRecruitingPhase 22025-11-28NCT04232085
European Rare Blood Disorders Platform (ENROL)Bone Marrow Failure, Bone Marrow Failure Disorders, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, Neoplasms by Histologic Type, Neoplasms by Site, Nutritional and Metabolic Diseases, anemia, bone marrow disorder, cardiovascular disorder, familial hemolytic anemia, hematologic disorder, hematopoietic and lymphoid system neoplasm, hemolytic anemia, hemorrhagic disease, hereditary disease, inherited hemoglobinopathy, iron metabolism disease, leukemia, lymphoid neoplasm, metabolic disease, neoplasm, plasma cell neoplasm, sickle cell disease, thalassemia, vascular disorder, vascular hemostatic diseaseRecruitingNot stated2024-02-09NCT06250595