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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Regenerative Medicine to Restore Hematopoiesis and Immune Function in Immunodeficiencies and Inherited Bone Marrow FailuresBone Marrow Failure, Bone Marrow Failure Disorders, Congenital Abnormalities, Congenital Bone Marrow Failure Syndromes, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, DNA repair disease, Fanconi anemia, Hemic and Lymphatic Diseases, Hoyeraal-Hreidarsson syndrome, Immune Deficiency Disease, Nutritional and Metabolic Diseases, Primary Immunodeficiency Diseases, Skin Abnormalities, Skin and Connective Tissue Diseases, X-linked disease, anemia, aplastic anemia, bone marrow disorder, dyskeratosis congenita, hematologic disorder, hereditary disease, hereditary skin disorder, immune system disorder, inborn error of immunity, inherited aplastic anemia, metabolic disease, skin disorder, telomere syndromeRecruitingPhase 22025-11-28NCT04232085

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Research sitesCityCountryLinked trials
Johns Hopkins UniversityBaltimoreUnited States150