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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Prevalence of Adrenal Insufficiency and Associated Factors in Rheumatoid Arthritis Patients Using Low-dose Corticosteroids.adrenal gland disorder, adrenocortical insufficiency, endocrine system disorderRecruitingNot stated2026-10-08NCT07866326
Home Exercise for Individuals With Neurodegenerative DiseaseBrain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Dyskinesias, Hereditary Central Nervous System Demyelinating Diseases, Leukoencephalopathies, Neurobehavioral Manifestations, Neurologic Manifestations, Nutritional and Metabolic Diseases, Pathological Conditions, Signs and Symptoms, Peroxisomal Disorders, Signs and Symptoms, X-linked disease, adrenal gland disorder, adrenocortical insufficiency, adrenoleukodystrophy, adrenomyeloneuropathy, atactic disorder, non-human animal, brain disorder, central nervous system disorder, cerebellar ataxia, cerebellar disorder, demyelinating disease, endocrine system disorder, hereditary disease, inborn errors of metabolism, inherited neurodegenerative disorder, intellectual disability, leukodystrophy, leukoencephalopathy with brain stem and spinal cord involvement-high lactate syndrome, metabolic disease, nervous system disorder, neurodegenerative diseaseRecruitingNot applicable2026-09-16NCT05443906
Long-term Follow-up of Participants With Cerebral Adrenoleukodystrophy Who Were Treated With Lenti-D Drug ProductBrain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Hereditary Central Nervous System Demyelinating Diseases, Leukoencephalopathies, Neurobehavioral Manifestations, Neurologic Manifestations, Nutritional and Metabolic Diseases, Peroxisomal Disorders, X-linked disease, adrenal gland disorder, adrenocortical insufficiency, adrenoleukodystrophy, brain disorder, central nervous system disorder, demyelinating disease, endocrine system disorder, hereditary disease, inborn errors of metabolism, inherited neurodegenerative disorder, intellectual disability, metabolic disease, nervous system disorderActive, not recruitingNot stated2026-09-14NCT02698579
A Block-and-Replace Therapy With Osilodrostat and Concomitant Glucocorticoid ReplacementCushing syndrome, adrenal gland disorder, adrenal gland hyperfunction, adrenocortical insufficiency, endocrine system disorder, endogenous Cushing syndromeRecruitingNot stated2026-09-09NCT06430528
Natural History Study of Patients With Excess AndrogenCongenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Familial Testotoxicosis, Female Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Male Urogenital Diseases, Nutritional and Metabolic Diseases, Urogenital Abnormalities, Urogenital Diseases, adrenal gland disorder, adrenocortical insufficiency, adrenogenital syndrome, classic congenital adrenal hyperplasia due to 21-hydroxylase deficiency, congenital adrenal hyperplasia, disorder of sexual differentiation, endocrine system disorder, gonadal disorder, hereditary disease, inborn errors of metabolism, metabolic disease, precocious puberty, steroid inherited metabolic disorderRecruitingNot stated2026-09-08NCT00250159
UCB Transplant of Inherited Metabolic Diseases With Administration of Intrathecal UCB Derived Oligodendrocyte-Like CellsBrain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, GM2 gangliosidosis, Gangliosidoses, Hemic and Lymphatic Diseases, Hereditary Central Nervous System Demyelinating Diseases, Krabbe disease, Leukoencephalopathies, Lipid Metabolism Disorders, Lipid Metabolism, Inborn Errors, Lysosomal Storage Diseases, Nervous System, Mannosidase Deficiency Diseases, Neurobehavioral Manifestations, Neurologic Manifestations, Neuronal Ceroid-Lipofuscinoses, Niemann-Pick disease, Niemann-Pick disease type A, Nutritional and Metabolic Diseases, Pelizaeus-Merzbacher spectrum disorder, Peroxisomal Disorders, Sandhoff disease, Skin and Connective Tissue Diseases, Sulfatidosis, Tay-Sachs disease, X-linked disease, adrenal gland disorder, adrenocortical insufficiency, adrenoleukodystrophy, alpha-mannosidosis, brain disorder, central nervous system disorder, connective tissue disorder, cutaneous mucinosis, demyelinating disease, endocrine system disorder, hereditary disease, histiocytosis, inborn carbohydrate metabolic disorder, inborn errors of metabolism, inherited neurodegenerative disorder, intellectual disability, juvenile neuronal ceroid lipofuscinosis, lymphatic system disorder, lysosomal lipid storage disorder, lysosomal storage disease, metabolic disease, metachromatic leukodystrophy, mucopolysaccharidosis, mucopolysaccharidosis type 2, nervous system disorder, neurodegenerative disease, non-Langerhans cell histiocytosis, sphingolipidosisRecruitingPhase 12026-09-03NCT02254863
IT and IV Lentiviral Gene Therapy for X-ALDBrain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Hereditary Central Nervous System Demyelinating Diseases, Leukoencephalopathies, Neurobehavioral Manifestations, Neurologic Manifestations, Nutritional and Metabolic Diseases, Peroxisomal Disorders, X-linked disease, adrenal gland disorder, adrenocortical insufficiency, adrenoleukodystrophy, brain disorder, central nervous system disorder, demyelinating disease, endocrine system disorder, hereditary disease, inborn errors of metabolism, inherited neurodegenerative disorder, intellectual disability, metabolic disease, nervous system disorderNot yet recruitingNot applicable2026-09-01NCT03727555
Quality of Life in Women With X-linked AdrenoleukodystrophyBrain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Hereditary Central Nervous System Demyelinating Diseases, Leukoencephalopathies, Neurobehavioral Manifestations, Neurologic Manifestations, Nutritional and Metabolic Diseases, Peroxisomal Disorders, X-linked disease, adrenal gland disorder, adrenocortical insufficiency, adrenoleukodystrophy, brain disorder, central nervous system disorder, demyelinating disease, endocrine system disorder, hereditary disease, inborn errors of metabolism, inherited neurodegenerative disorder, intellectual disability, metabolic disease, nervous system disorderRecruitingNot stated2026-08-27NCT04675749
Pharmacokinetics, Pharmacodynamics, and Safety Profile of Understudied Drugs Administered to Children Per Standard of Care (POPS)Abnormalities, Multiple, Arrhythmias, Cardiac, COVID-19, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Coronaviridae Infections, Down syndrome, Dyssomnias, Edema, Female Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Genital Diseases, Hemic and Lymphatic Diseases, Hemorrhage, Infant, Newborn, Diseases, Infant, Premature, Diseases, Infections, Inflammation, Kawasaki disease, Lung Injury, Menorrhagia, Menstruation Disturbances, Neurobehavioral Manifestations, Neurologic Manifestations, Nidovirales infectious disease, Nutritional and Metabolic Diseases, Orthocoronavirinae infectious disease, Pain, Pathologic Processes, Pathological Conditions, Signs and Symptoms, RNA Virus Infections, Signs and Symptoms, Skin and Connective Tissue Diseases, Sleep Disorders, Intrinsic, Suppuration, Urogenital Diseases, Uterine Hemorrhage, Ventilator-Induced Lung Injury, Water-Electrolyte Imbalance, adrenal gland disorder, adrenal gland hyperfunction, adrenocortical insufficiency, attention deficit hyperactivity disorder, inattentive type, blood coagulation disease, bronchopulmonary dysplasia, cardiovascular disorder, cellulitis, chromosomal disorder, coagulation protein disease, connective tissue disorder, endocrine system disorder, female reproductive system disorder, heart disorder, heart failure, hematologic disorder, hemophilia A, hemorrhagic disease, hereditary disease, hyperaldosteronism, hyperphosphatemia, hypertensive disorder, inherited blood coagulation disorder, insomnia, intellectual disability, lung disorder, lymphatic system disorder, metabolic disease, nervous system disorder, neurodevelopmental disorder, oppositional defiant disorder, pediatric multisystem inflammatory disease, COVID-19 related, phosphorus metabolism disease, pneumonia, potassium deficiency disease, primary aldosteronism, psychiatric disorder, pulmonary arterial hypertension, pulmonary hypertension, respiratory system disorder, respiratory tract infectious disorder, skin disorder, skin disorder caused by infection, skin infection, skin vascular disease, sleep-wake disorder, uterine disorder, vascular disorder, vascular hemostatic disease, vasculitis, viral infectious disease, viral pneumoniaRecruitingNot stated2026-08-21NCT04278404
Evaluation of Children With Endocrine and Metabolic-Related ConditionsBody Weight, Bone Diseases, Metabolic, Nutritional and Metabolic Diseases, Overweight, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Signs and Symptoms, adrenal gland disorder, adrenocortical insufficiency, bone disorder, endocrine system disorder, hereditary endocrine growth disease, metabolic disease, musculoskeletal system disorder, nutritional disorder, obesity disorder, overnutritionRecruitingNot stated2026-08-13NCT02769975
Natural History of Sphingosine Phosphate Lyase Insufficiency Syndrome (SPLIS)Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Charcot-Marie-Tooth disease, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Female Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Infant, Newborn, Diseases, Lipid Metabolism Disorders, Lipid Metabolism, Inborn Errors, Lysosomal Storage Diseases, Nervous System, Male Urogenital Diseases, Nutritional and Metabolic Diseases, Primary Immunodeficiency Diseases, Skin Abnormalities, Skin and Connective Tissue Diseases, Urogenital Diseases, adrenal gland disorder, adrenocortical insufficiency, autoimmune disease, brain disorder, central nervous system disorder, central nervous system malformation, endocrine system disorder, hereditary disease, hereditary motor and sensory neuropathy, hypothyroidism, ichthyosis, immune system disorder, inborn error of immunity, inborn errors of metabolism, inherited neurodegenerative disorder, keratosis, kidney disorder, lysosomal lipid storage disorder, lysosomal storage disease, metabolic disease, nephrosis, nephrotic syndrome, nervous system disorder, neurodegenerative disease, neuromuscular disease, peripheral nervous system disorder, polyneuropathy, skin disorder, sphingolipidosis, thyroid gland disorder, urinary system disorderRecruitingNot stated2026-08-04NCT06669949
Telehealth Music Therapy for Adults With Endocrine Disorder and DepressionGraves disease, Hashimoto thyroiditis, Nutritional and Metabolic Diseases, Polyendocrinopathies, Autoimmune, Polyglandular Type III Autoimmune Syndrome, adrenal gland disorder, adrenocortical insufficiency, autoimmune disease, autoimmune thyroid disease, depressive disorder, diabetes mellitus, disease of orbital part of eye adnexa, endocrine system disorder, exophthalmos, eye disorder, glucose metabolism disease, goiter, hyperthyroidism, immune system disorder, metabolic disease, thyroid gland disorder, thyroiditis, type 1 diabetes mellitusRecruitingNot applicable2026-07-30NCT07413874
Evaluation of Circadian Hormonal Balance: LC-MS/MS Measurement of Salivary and Serum Steroids in Patients With Congenital Adrenal Hyperplasia46,XX disorder of sex development, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Female Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Hyperandrogenism, Male Urogenital Diseases, Nutritional and Metabolic Diseases, Urogenital Abnormalities, Urogenital Diseases, adrenal gland disorder, adrenocortical insufficiency, adrenogenital syndrome, classic congenital adrenal hyperplasia due to 21-hydroxylase deficiency, congenital adrenal hyperplasia, disorder of sexual differentiation, endocrine system disorder, gonadal disorder, hereditary disease, inborn errors of metabolism, metabolic disease, steroid inherited metabolic disorderNot yet recruitingNot stated2026-07-21NCT07718230
Hydrocortisone Versus Methylprednisolone for the Treatment of Glucocorticoid-Induced Adrenal Insufficiencyadrenal gland disorder, adrenocortical insufficiency, endocrine system disorderNot yet recruitingPhase 42026-07-14NCT07703098
Treating Leg Symptoms in Women With X-linked AdrenoleukodystrophyBrain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Dyssomnias, Hereditary Central Nervous System Demyelinating Diseases, Leukoencephalopathies, Neurobehavioral Manifestations, Neurologic Manifestations, Nutritional and Metabolic Diseases, Parasomnias, Peroxisomal Disorders, Sleep Disorders, Intrinsic, X-linked disease, adrenal gland disorder, adrenocortical insufficiency, adrenoleukodystrophy, brain disorder, central nervous system disorder, demyelinating disease, endocrine system disorder, hereditary disease, inborn errors of metabolism, inherited neurodegenerative disorder, intellectual disability, metabolic disease, nervous system disorder, psychiatric disorder, restless legs syndrome, sleep-wake disorderActive, not recruitingPhase 42026-07-01NCT05003648
Combination Osilodrostat and Cabergoline in Cushing's Disease46,XX disorder of sex development, ACTH-dependent Cushing syndrome, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Female Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Hyperandrogenism, Male Urogenital Diseases, Nutritional and Metabolic Diseases, Urogenital Abnormalities, Urogenital Diseases, Water-Electrolyte Imbalance, adrenal gland disorder, adrenocortical insufficiency, adrenogenital syndrome, brain disorder, cardiovascular disorder, central nervous system disorder, disorder of sexual differentiation, endocrine system disorder, gonadal disorder, hyperpituitarism, hypertensive disorder, hypothalamic disorder, metabolic disease, nervous system disorder, pituitary gland disorder, potassium deficiency disease, vascular disorderEnrolling by invitationPhase 42026-05-22NCT07603466
Genomic and Metabolomic Markers Reflecting the Complications of Hypercortisolism (CUSHINGOMICS)Cushing syndrome, adrenal gland disorder, adrenal gland hyperfunction, adrenocortical insufficiency, endocrine system disorderActive, not recruitingNot applicable2026-05-20NCT04840693
Adrenoleukodystrophy National Registry StudyBrain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Hereditary Central Nervous System Demyelinating Diseases, Leukoencephalopathies, Neurobehavioral Manifestations, Neurologic Manifestations, Nutritional and Metabolic Diseases, Peroxisomal Disorders, X-linked disease, adrenal gland disorder, adrenocortical insufficiency, adrenoleukodystrophy, brain disorder, central nervous system disorder, demyelinating disease, endocrine system disorder, hereditary disease, inborn errors of metabolism, inherited neurodegenerative disorder, intellectual disability, metabolic disease, nervous system disorderRecruitingNot stated2026-05-12NCT03789721
A Swiss Assessment of Hypothalamic-pituitary-adrenal Axis Suppression After Glucocorticoid Therapy for Leukemia and Lymphoblastic Lymphoma in ChildrenHemic and Lymphatic Diseases, Neoplasms by Histologic Type, Precursor Cell Lymphoblastic Leukemia-Lymphoma, adrenal gland disorder, adrenocortical insufficiency, endocrine system disorder, hematologic disorder, immune system disorder, immunoproliferative disorder, leukemia, lymphatic system disorder, lymphoid leukemia, lymphoproliferative syndrome, neoplasmRecruitingNot stated2026-05-08NCT06861530
Screening and Stimulation Testing for Residual Secretion of Adrenal Steroid Hormones in Autoimmune Addison's Diseaseadrenal gland disorder, adrenocortical insufficiency, autoimmune disease, endocrine system disorder, immune system disorderActive, not recruitingNot applicable2026-05-08NCT03793114
Study on the Incidence of Adrenal Insufficiency After Surgery in Primary Aldosteronism Patients Concurrent With or Without Autonomous Cortisol Secretionadrenal gland disorder, adrenal gland hyperfunction, adrenocortical insufficiency, endocrine system disorder, hyperaldosteronism, primary aldosteronismRecruitingNot stated2026-05-01NCT06955286
A Study to Investigate OCS Tapering in Adult Participants With Generalized Myasthenia Gravis Treated With RavulizumabNeoplasms by Site, Paraneoplastic Syndromes, Nervous System, adrenal gland disorder, adrenocortical insufficiency, autoimmune disease, autoimmune disorder of the nervous system, endocrine system disorder, generalized myasthenia gravis, immune system disorder, myasthenia gravis, neoplasm, nervous system disorder, neurodegenerative disease, neuromuscular disease, neuromuscular junction disease, paraneoplastic syndromeRecruitingPhase 42026-04-09NCT07221838
Effect of Supplemental Hydrocortisone During Stress in Prednisolone-induced Adrenal InsufficiencySkin and Connective Tissue Diseases, adrenal gland disorder, adrenocortical insufficiency, arteritis, autoimmune disease, autoimmune disorder of the nervous system, brain disorder, cardiovascular disorder, central nervous system disorder, central nervous system vasculitis, cerebrovascular disorder, connective tissue disorder, endocrine system disorder, immune system disorder, muscle tissue disorder, musculoskeletal system disorder, nervous system disorder, polymyalgia rheumatica, rheumatic disorder, skin disorder, skin vascular disease, temporal arteritis, vascular disorder, vasculitisRecruitingPhase 42026-03-16NCT05435781
Updated Diagnostic Cortisol Values for Adrenal Insufficiencyadrenal gland disorder, adrenocortical insufficiency, endocrine system disorderRecruitingNot applicable2026-02-19NCT05149638
Risks of Ramadan Fasting in Patients With Primary Adrenal Insufficiency Treated With Prednisolone.Dehydration, Nutritional and Metabolic Diseases, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Water-Electrolyte Imbalance, adrenal gland disorder, adrenocortical insufficiency, autoimmune disease, cardiovascular disorder, endocrine system disorder, glucose metabolism disease, hypoglycemia, hypotensive disorder, immune system disorder, metabolic disease, vascular disorderNot yet recruitingNot applicable2026-01-26NCT07367425