Swipe the table sideways for more columns.

TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Long-term Follow-up of Participants With Cerebral Adrenoleukodystrophy Who Were Treated With Lenti-D Drug ProductBrain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Hereditary Central Nervous System Demyelinating Diseases, Leukoencephalopathies, Neurobehavioral Manifestations, Neurologic Manifestations, Nutritional and Metabolic Diseases, Peroxisomal Disorders, X-linked disease, adrenal gland disorder, adrenocortical insufficiency, adrenoleukodystrophy, brain disorder, central nervous system disorder, demyelinating disease, endocrine system disorder, hereditary disease, inborn errors of metabolism, inherited neurodegenerative disorder, intellectual disability, metabolic disease, nervous system disorderActive, not recruitingNot stated2026-09-14NCT02698579

1 results · Page 1 of 1

Swipe the table sideways for more columns.

OrganizationsLinked trials
Genetix Biotherapeutics Inc.7

13 results · Page 1 of 1

Swipe the table sideways for more columns.

Research sitesCityCountryLinked trials
Boston Children's Hospital/Massachusetts General HospitalBostonUnited States1
Great Ormond Street HospitalLondonUnited Kingdom1
Hospital das Clínicas da Universidade de São PauloSão PauloBrazil1
Hôpital BicêtreLe Kremlin-BicêtreFrance1
Instituto NeurogeniaCabaArgentina1
Lucile Packard Children's Hospital - StanfordPalo AltoUnited States3
Mattel Children's Hospital-UCLALos AngelesUnited States1
Ospedale Pediatrico Bambino GesùRomeItaly1
Prinses Maxima CenterUtrechtNetherlands1
Royal Free London HospitalLondonUnited Kingdom1
University of MinnesotaMinneapolisUnited States325
Universitätsklinikum Leipzig AöRLeipzigGermany4
Women's and Children's HospitalNorth AdelaideAustralia2