thalassemia
thalassemia
Explore linked clinical trials. Standard reference: MONDO:000098496 results · Page 1 of 4
Clinical trials
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| Trial | Conditions | Status | Phase | Updated | More info | NCT ID |
|---|---|---|---|---|---|---|
| Collection of Human Biospecimens for Basic and Clinical Research Into Globin Variants | Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, Infections, Mosquito-Borne Diseases, anemia, beta thalassemia, familial hemolytic anemia, hematologic disorder, hemolytic anemia, hereditary disease, inherited hemoglobinopathy, malaria, parasitic infectious disease, protozoa infectious disease, sickle cell disease, thalassemia, vector-borne disease | Recruiting | Not stated | 2026-10-02 | NCT03937817 | |
| A Study to Provide Access to Mitapivat for Participants Who Previously Participated in an Agios-Sponsored Mitapivat Study | Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, anemia, familial hemolytic anemia, hematologic disorder, hemolytic anemia, hereditary disease, inherited hemoglobinopathy, pyruvate kinase deficiency of red cells, sickle cell disease, thalassemia | Enrolling by invitation | Phase 4 | 2026-09-29 | NCT05777993 | |
| Determination of Red Cell Survival in Sickle Cell Disease and Other Hemoglobinopathies Using Biotin Labeling | Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, anemia, familial hemolytic anemia, hematologic disorder, hemolytic anemia, hereditary disease, inherited hemoglobinopathy, sickle cell disease, thalassemia | Recruiting | Early phase 1 | 2026-09-28 | NCT06313398 | |
| ALS20-101 Lentiviral Gene Therapy for Beta Thalassemia | Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, anemia, beta thalassemia, familial hemolytic anemia, hematologic disorder, hemolytic anemia, hereditary disease, inherited hemoglobinopathy, thalassemia | Recruiting | Phase 1 / Phase 2 | 2026-09-23 | NCT06364774 | |
| Growth Evaluation, Health Promotion, and Clinical Management in Children and Adolescents With Thalassemia | Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, Puberty, Delayed, Thalassemia Intermedia, Thalassemia Major, anemia, beta thalassemia, endocrine system disorder, familial hemolytic anemia, gonadal disorder, hematologic disorder, hemolytic anemia, hereditary disease, inherited hemoglobinopathy, thalassemia | Active, not recruiting | Not applicable | 2026-09-18 | NCT06931912 | |
| A Research Study Looking at Long-term Treatment With Etavopivat in People With Sickle Cell Disease or Thalassaemia | Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, anemia, familial hemolytic anemia, hematologic disorder, hemolytic anemia, hereditary disease, inherited hemoglobinopathy, sickle cell disease, thalassemia | Recruiting | Phase 3 | 2026-09-18 | NCT06609226 | |
| A Study to Determine the Efficacy and Safety of Luspatercept in Adult Participants and to Evaluate the Safety and Pharmacokinetics in and Adolescent Participants With Alpha (α)-Thalassemia | Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, alpha thalassemia spectrum, anemia, familial hemolytic anemia, hematologic disorder, hemolytic anemia, hereditary disease, inherited hemoglobinopathy, thalassemia | Active, not recruiting | Phase 2 | 2026-09-10 | NCT05664737 | |
| Improving the Results of Bone Marrow Transplantation for Patients With Severe Congenital Anemias | Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, anemia, beta thalassemia, familial hemolytic anemia, hematologic disorder, hemolytic anemia, hereditary disease, inherited hemoglobinopathy, sickle cell disease, thalassemia | Active, not recruiting | Phase 1 / Phase 2 | 2026-09-09 | NCT00061568 | |
| Partial Stem Cell Transplant for Sickle Cell Disease From Matched Donors | Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, anemia, beta thalassemia, familial hemolytic anemia, hematologic disorder, hemolytic anemia, hereditary disease, inherited hemoglobinopathy, sickle cell disease, thalassemia | Recruiting | Phase 1 / Phase 2 | 2026-09-04 | NCT07599176 | |
| International Registry of Patients With Alpha Thalassemia | Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, alpha thalassemia spectrum, anemia, familial hemolytic anemia, hematologic disorder, hemolytic anemia, hereditary disease, inherited hemoglobinopathy, thalassemia | Recruiting | Not stated | 2026-09-02 | NCT04872179 | |
| Clinical, Economic,and Psychosocial Burden of Thalassemia in Sohag | Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, anemia, familial hemolytic anemia, hematologic disorder, hemolytic anemia, hereditary disease, inherited hemoglobinopathy, thalassemia | Not yet recruiting | Not stated | 2026-08-31 | NCT07796022 | |
| A Study to Evaluate the Safety and Effectiveness of Luspatercept for the Treatment of Transfusion-dependent (TD) Anemia Associated With Myelodysplastic Syndromes (MDS) & Beta-thalassemia (β-Thal) in India | Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, anemia, beta thalassemia, bone marrow disorder, familial hemolytic anemia, hematologic disorder, hemolytic anemia, hereditary disease, inherited hemoglobinopathy, thalassemia | Active, not recruiting | Phase 4 | 2026-08-31 | NCT05891249 | |
| Gene Therapy of Beta Thalassemia Using a Self-inactivating Lentiviral Vector | Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, anemia, beta thalassemia, familial hemolytic anemia, hematologic disorder, hemolytic anemia, hereditary disease, inherited hemoglobinopathy, thalassemia | Not yet recruiting | Not applicable | 2026-08-27 | NCT03351829 | |
| A Gene Transfer Study Inducing Fetal Hemoglobin in Sickle Cell Disease (GRASP, BMT CTN 2001) | Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, anemia, beta thalassemia, familial hemolytic anemia, hematologic disorder, hemolytic anemia, hereditary disease, inherited hemoglobinopathy, sickle cell disease, thalassemia | Active, not recruiting | Phase 2 | 2026-08-25 | NCT05353647 | |
| CINC424A2X01B Rollover Protocol | Bronchiolitis Obliterans, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, Myeloproliferative Disorders, Neoplasms by Histologic Type, Neoplasms by Site, acquired polycythemia vera, acute myeloid leukemia, anemia, bone marrow disorder, bone marrow neoplasm, bronchial disorder, bronchiolitis, bronchiolitis obliterans syndrome, bronchitis, cryptogenic organizing pneumonia, familial hemolytic anemia, graft versus host disease, hematologic disorder, hematopoietic and lymphoid system neoplasm, hemolytic anemia, hereditary disease, immune system disorder, inherited hemoglobinopathy, leukemia, lung disorder, myeloid leukemia, neoplasm, obstructive lung disease, primary myelofibrosis, respiratory system disorder, thalassemia | Active, not recruiting | Phase 4 | 2026-08-20 | NCT02386800 | |
| Nonmyeloablative Peripheral Blood Mobilized Hematopoietic Precursor Cell Transplantation for Sickle Cell Disease and Beta-thalassemia in People With Higher Risk of Transplant Failure | Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, anemia, familial hemolytic anemia, graft versus host disease, hematologic disorder, hemolytic anemia, hereditary disease, immune system disorder, inherited hemoglobinopathy, sickle cell disease, thalassemia | Active, not recruiting | Phase 2 | 2026-08-18 | NCT02105766 | |
| ATHN Transcends: A Natural History Study of Non-Neoplastic Hematologic Disorders | Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Embolism and Thrombosis, Hemic and Lymphatic Diseases, Skin and Connective Tissue Diseases, X-linked disease, anemia, blood coagulation disease, blood platelet disease, cardiovascular disorder, coagulation protein disease, connective tissue disorder, familial hemolytic anemia, hematologic disorder, hemolytic anemia, hemophilia A, hemophilia B, hemorrhagic disease, hereditary disease, inherited blood coagulation disorder, inherited hemoglobinopathy, sickle cell disease, thalassemia, thrombophilia, thrombotic disease, vascular disorder, vascular hemostatic disease, von Willebrand disease (hereditary or acquired) | Recruiting | Not stated | 2026-08-17 | NCT04398628 | |
| T-Cell Depleted Alternative Donor Bone Marrow Transplant for Sickle Cell Disease (SCD) and Other Anemias | Bone Marrow Failure Disorders, Congenital Bone Marrow Failure Syndromes, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Diamond-Blackfan anemia, Hemic and Lymphatic Diseases, anemia, aplastic anemia, beta thalassemia, beta-thalassemia major, bone marrow disorder, familial hemolytic anemia, hematologic disorder, hemolytic anemia, hereditary disease, inherited aplastic anemia, inherited hemoglobinopathy, pure red-cell aplasia, sickle cell disease, thalassemia | Recruiting | Phase 1 / Phase 2 | 2026-08-13 | NCT03653338 | |
| A Long-term Follow-up Study in Participants Who Received CTX001 | Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, anemia, beta thalassemia, familial hemolytic anemia, hematologic disorder, hemolytic anemia, hereditary disease, inherited hemoglobinopathy, sickle cell disease, thalassemia | Enrolling by invitation | Phase 3 | 2026-08-11 | NCT04208529 | |
| Safety and Efficacy of Hemoglobin F Inducers in Patients With Beta Thalassemia | Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, anemia, familial hemolytic anemia, hematologic disorder, hemolytic anemia, hereditary disease, inherited hemoglobinopathy, thalassemia | Recruiting | Not applicable | 2026-08-06 | NCT07673302 | |
| Low-Dose Liposomal Amphotericin B for Invasive Fungal Infection Prophylaxis in Neutropenic Children | Bacterial Infections and Mycoses, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Cytopenia, Hemic and Lymphatic Diseases, Infections, Invasive Fungal Infections, agranulocytosis, anemia, familial hemolytic anemia, fungal infectious disease, graft versus host disease, hematologic disorder, hemolytic anemia, hereditary disease, immune system disorder, inherited hemoglobinopathy, leukocyte disorder, leukopenia, neutropenia, thalassemia | Recruiting | Not stated | 2026-07-24 | NCT07725263 | |
| Gene Therapy for Patients With Transfusion-Dependent β-Thalassemia | Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, anemia, beta thalassemia, familial hemolytic anemia, hematologic disorder, hemolytic anemia, hereditary disease, inherited hemoglobinopathy, thalassemia | Not yet recruiting | Phase 2 | 2026-07-23 | NCT07721480 | |
| Effect of Exercise on Body Composition and Bone Health in Patients With Thalassemia | Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, anemia, familial hemolytic anemia, hematologic disorder, hemolytic anemia, hereditary disease, inherited hemoglobinopathy, thalassemia | Active, not recruiting | Not applicable | 2026-07-22 | NCT07064941 | |
| Long-term Follow-up Study of BRL-101 for TDT | Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, anemia, beta thalassemia, familial hemolytic anemia, hematologic disorder, hemolytic anemia, hereditary disease, inherited hemoglobinopathy, thalassemia | Recruiting | Not stated | 2026-07-21 | NCT06298630 | |
| Safety and Efficacy Evaluation of BRL-101 in Subjects With Transfusion-Dependent β-Thalassemia | Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, anemia, beta thalassemia, familial hemolytic anemia, hematologic disorder, hemolytic anemia, hereditary disease, inherited hemoglobinopathy, thalassemia | Active, not recruiting | Phase 1 / Phase 2 | 2026-07-21 | NCT05577312 |