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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
A Long-term Follow-up Study in Participants Who Received CTX001Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, anemia, beta thalassemia, familial hemolytic anemia, hematologic disorder, hemolytic anemia, hereditary disease, inherited hemoglobinopathy, sickle cell disease, thalassemiaEnrolling by invitationPhase 32026-08-11NCT04208529

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Research sitesCityCountryLinked trials
Ann & Robert H. Lurie Children's Hospital of Chicago - HematologyChicagoUnited States2
Center for Pediatric Clinical Studies (CPCS)Klinik Für Kinder- Und JugendmedizinGermany1
Great Ormond Street Hospital for ChildrenLondonUnited Kingdom15
Hammersmith Hospital - Haematology DeptLondonUnited Kingdom1
Herbert Irving Pavilion - HematologyNew YorkUnited States1
Hopital Universitaire des Enfants Reine Fabiola (HUDERF) - HematologyBrusselsBelgium1
Hospital for Sick Children - HematologyTorontoCanada2
IRCSS Ospedale Pediatrico Bambino Gesu - Dipartimento di Onco-Ematologia e Terapia Cellulare e GenicaRomeItaly4
Levine Children's Hospital - HematologyCharlotteUnited States3
Lucile Packard Children's HospitalPalo AltoUnited States24
Methodist Healthcare System of San Antonio, Methodist Hospital, Methodist Children's HospitalSan AntonioUnited States1
New York Presbyterian Hospital - Morgan Stanley Children's HospitalNew YorkUnited States2
Regensburg University Hospital, Clinic and Polyclinic for Paediatric and Adolescent MedicineRegensburgGermany1
St. Jude Children's Research HospitalMemphisUnited States194
St. Paul's Hospital - HematologyVancouverCanada1
The Children's Hospital of Philadelphia - HematologyPhiladelphiaUnited States2
Toronto General Hospital - HematologyTorontoCanada1
TriStar Medical Group Children's Specialists - Pediatric OncologyNashvilleUnited States4
University College London Hospital NHS Foundation - MainLondonUnited Kingdom1
University Hospital Duesseldorf - Department of Pediatric Oncology, Hematology and Clinical ImmunologyDüsseldorfGermany2