neuroaxonal dystrophy
neuroaxonal dystrophy
Explore linked clinical trials. Standard reference: MONDO:00022835 results · Page 1 of 1
Clinical trials
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| Trial | Conditions | Status | Phase | Updated | More info | NCT ID |
|---|---|---|---|---|---|---|
| Brain Iron in Beta-Propeller Protein Associated Neurodegeneration (BPAN) | Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Nerve Degeneration, Nutritional and Metabolic Diseases, Pathologic Processes, Pathological Conditions, Signs and Symptoms, basal ganglia disorder, brain disorder, central nervous system disorder, hereditary disease, inherited neurodegenerative disorder, iron metabolism disease, metabolic disease, movement disorder, nervous system disorder, neuroaxonal dystrophy, neurodegeneration with brain iron accumulation, neurodegenerative disease, pantothenate kinase-associated neurodegeneration | Not yet recruiting | Not applicable | 2026-10-09 | NCT07868120 | |
| Neurodegenerative Diseases Progression Markers (MARKERS-NDD) | Alzheimer disease, Cognition Disorders, Cognitive Dysfunction, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Frontotemporal Lobar Degeneration, Lewy body dementia, Neurologic Manifestations, Nutritional and Metabolic Diseases, Ocular Motility Disorders, Parkinson disease, Pathological Conditions, Signs and Symptoms, Signs and Symptoms, TDP-43 proteinopathy, amyotrophic lateral sclerosis, autonomic nervous system disorder, basal ganglia disorder, brain disorder, central nervous system disorder, cognitive disorder, corticobasal degeneration disorder, cranial nerve neuropathy, dementia, eye disorder, hereditary disease, inherited neurodegenerative disorder, iron metabolism disease, iron poisoning, metabolic disease, motor neuron disorder, movement disorder, multiple system atrophy, nervous system disorder, neuroaxonal dystrophy, neurodegeneration with brain iron accumulation, neurodegenerative disease, neuromuscular disease, ophthalmoplegia, palsy, pantothenate kinase-associated neurodegeneration, parkinsonian disorder, primary dysautonomia, proteostasis deficiencies, psychiatric disorder, spinal cord disorder, synucleinopathy, tauopathy | Recruiting | Not stated | 2026-09-02 | NCT06596746 | |
| Superiority Trial Evaluating Digitalized Information Media for Patients With Advanced Sarcomas Receiving Systemic Treatment. | Neoplasms by Histologic Type, Neoplasms, Connective and Soft Tissue, brain disorder, central nervous system disorder, neoplasm, nervous system disorder, neuroaxonal dystrophy, sarcoma | Recruiting | Not applicable | 2026-03-18 | NCT06211257 | |
| TIRCON International NBIA Registry | Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Familial apoceruloplasmin deficiency, Kufor-Rakeb syndrome, Woodhouse-Sakati syndrome, aceruloplasminemia, basal ganglia disorder, brain disorder, central nervous system disorder, fatty acid hydroxylase-associated neurodegeneration, hereditary disease, inherited neurodegenerative disorder, movement disorder, nervous system disorder, neuroaxonal dystrophy, neurodegeneration with brain iron accumulation, neurodegenerative disease, neuroferritinopathy, pantothenate kinase-associated neurodegeneration | Recruiting | Not stated | 2025-06-05 | NCT05522374 | |
| A Study to Assess Efficacy and Safety of RT001 in Subjects With Infantile Neuroaxonal Dystrophy | brain disorder, central nervous system disorder, nervous system disorder, neuroaxonal dystrophy, neurodegeneration with brain iron accumulation 2A | Active, not recruiting | Phase 2 / Phase 3 | 2021-10-14 | NCT03570931 |