hypochondroplasia
hypochondroplasia
Explore linked clinical trials. Standard reference: MONDO:000779310 results ยท Page 1 of 1
Clinical trials
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| Trial | Conditions | Status | Phase | Updated | More info | NCT ID |
|---|---|---|---|---|---|---|
| Prospective Longitudinal Multicentric Study to Measure Limb Movement in Patients With FGFR3-related Skeletal Dysplasia | Bone Diseases, Developmental, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Dwarfism, achondroplasia, bone disorder, hereditary disease, hypochondroplasia, musculoskeletal system disorder, osteochondrodysplasia | Recruiting | Not stated | 2026-09-23 | NCT07388966 | |
| Long-Term Extension Study of Vosoritide to Treat Children With Hypochondroplasia | hypochondroplasia | Enrolling by invitation | Phase 3 | 2026-09-09 | NCT07073014 | |
| Open-Label, Long-Term, Extension Study of Infigratinib in Children With Hypochondroplasia | Bone Diseases, Developmental, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Dwarfism, Nutritional and Metabolic Diseases, Skin and Connective Tissue Diseases, bone disorder, connective tissue disorder, cutaneous mucinosis, endocrine system disorder, hereditary disease, hypochondroplasia, inborn carbohydrate metabolic disorder, inborn errors of metabolism, lysosomal storage disease, metabolic disease, mucopolysaccharidosis, mucopolysaccharidosis type 4, musculoskeletal system disorder, osteochondrodysplasia | Enrolling by invitation | Phase 2 | 2026-08-26 | NCT07393373 | |
| An Interventional Study of Infigratinib in Children With Hypochondroplasia | Bone Diseases, Developmental, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Dwarfism, Nutritional and Metabolic Diseases, Skin and Connective Tissue Diseases, bone disorder, connective tissue disorder, cutaneous mucinosis, endocrine system disorder, hereditary disease, hypochondroplasia, inborn carbohydrate metabolic disorder, inborn errors of metabolism, lysosomal storage disease, metabolic disease, mucopolysaccharidosis, mucopolysaccharidosis type 4, musculoskeletal system disorder, osteochondrodysplasia | Enrolling by invitation | Phase 2 / Phase 3 | 2026-07-16 | NCT06873035 | |
| Prospective Clinical Assessment Study in Children With Hypochondroplasia | Bone Diseases, Developmental, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Dwarfism, Nutritional and Metabolic Diseases, Skin and Connective Tissue Diseases, bone disorder, connective tissue disorder, cutaneous mucinosis, endocrine system disorder, hereditary disease, hypochondroplasia, inborn carbohydrate metabolic disorder, inborn errors of metabolism, lysosomal storage disease, metabolic disease, mucopolysaccharidosis, mucopolysaccharidosis type 4, musculoskeletal system disorder, osteochondrodysplasia | Recruiting | Not stated | 2026-07-16 | NCT06410976 | |
| A Study of Vosoritide Versus Placebo in Children With Hypochondroplasia Aged 0 to < 36 Months | hypochondroplasia | Recruiting | Phase 2 | 2026-03-31 | NCT07126262 | |
| Vosoritide for Selected Genetic Causes of Short Stature | Bone Diseases, Developmental, Cardiovascular Abnormalities, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Craniofacial Abnormalities, Dwarfism, Musculoskeletal Abnormalities, Noonan syndrome, Skin and Connective Tissue Diseases, bone disorder, cardiovascular disorder, congenital heart disease, connective tissue disorder, endocrine system disorder, heart disorder, hereditary disease, hypochondroplasia, musculoskeletal system disorder | Active, not recruiting | Phase 2 | 2026-03-18 | NCT04219007 | |
| Interventional Study of Vosoritide for the Treatment of Children With Hypochondroplasia | Bone Diseases, Developmental, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Dwarfism, bone disorder, endocrine system disorder, hereditary disease, hypochondroplasia, musculoskeletal system disorder, osteochondrodysplasia | Active, not recruiting | Phase 3 | 2026-01-20 | NCT06455059 | |
| A Multicenter Multinational Observational Study of Children With Hypochondroplasia | hypochondroplasia | Recruiting | Not stated | 2025-04-03 | NCT06212947 | |
| Registry for Patients With Achondroplasia / Hypochondroplasia (OMPR-Ach/Hy) | Bone Diseases, Developmental, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Dwarfism, achondroplasia, bone disorder, hereditary disease, hypochondroplasia, musculoskeletal system disorder, osteochondrodysplasia | Recruiting | Not stated | 2022-04-28 | NCT05328050 |