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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
An Interventional Study of Infigratinib in Children With HypochondroplasiaBone Diseases, Developmental, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Dwarfism, Nutritional and Metabolic Diseases, Skin and Connective Tissue Diseases, bone disorder, connective tissue disorder, cutaneous mucinosis, endocrine system disorder, hereditary disease, hypochondroplasia, inborn carbohydrate metabolic disorder, inborn errors of metabolism, lysosomal storage disease, metabolic disease, mucopolysaccharidosis, mucopolysaccharidosis type 4, musculoskeletal system disorder, osteochondrodysplasiaEnrolling by invitationPhase 2 / Phase 32026-07-16NCT06873035

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OrganizationsLinked trials
QED Therapeutics, a BridgeBio company5

24 results · Page 1 of 1

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Research sitesCityCountryLinked trials
Astrid Lindgren Children's HospitalSolnaSweden1
Centre Hospitalier Universitaire (CHU) de Toulouse - Hôpital des EnfantsToulouseFrance1
Children's Hospital of Eastern Ontario Research InstituteOttawaCanada5
Children's National HospitalWashington D.C.United States100
Childrens Hospital ColoradoAuroraUnited States23
Cincinnati Children's Hospital Medical CenterCincinnatiUnited States405
Glasgow Clinical Research Facility, Queen Elizabeth University HospitalGlasgowUnited Kingdom3
Haukeland University HospitalBergenNorway2
Hospital Pediátrico de CoimbraCoimbraPortugal1
Hôpital Femme Mère EnfantBronFrance1
Hôpital Universitaire Necker-Enfants MaladesParisFrance1
Johns Hopkins School of MedicineBaltimoreUnited States21
KK Women's and Children's HospitalSingaporeSingapore8
London Health Services Centre - Children's Hospital of Western OntarioLondonCanada1
Manchester UniversityManchesterUnited Kingdom3
Murdoch Children's Research Institute - The Royal Children's Hospital MelbourneParkvilleAustralia3
Paediatric Clinical Research Unit at Oslo University HospitalOsloNorway1
Sheffield Children's HospitalSheffieldUnited Kingdom2
UCSF Benioff Children's HospitalOaklandUnited States10
Unidad de Cirugía Artroscopica, Hopsital MIKSVitoria-GasteizSpain1
University of MissouriColumbiaUnited States9
University of Wisconsin Madison - Waisman Center Bone Dysplasia ClinicMadisonUnited States4
Université de Montréal - Centre Hospitalier Universitaire Sainte-JustineMontrealCanada4
Vanderbilt University Medical CenterNashvilleUnited States427