progressive familial intrahepatic cholestasis type 1
progressive familial intrahepatic cholestasis type 1
Explore linked clinical trials. Standard reference: MONDO:000889213 results · Page 1 of 1
Clinical trials
Swipe the table sideways for more columns.
| Trial | Conditions | Status | Phase | Updated | More info | NCT ID |
|---|---|---|---|---|---|---|
| Pediatric Evaluation and Registry for Liver Cholestasis in Canada | Abnormalities, Multiple, Alagille syndrome, Cardiovascular Abnormalities, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, bile duct disorder, biliary tract disorder, cardiovascular disorder, cholestasis, congenital heart disease, hereditary disease, intrahepatic cholestasis, liver disorder, progressive familial intrahepatic cholestasis type 1 | Recruiting | Not stated | 2026-10-08 | NCT07411716 | |
| Long-Term SafEty and Clinical Outcomes of LivmArli in Patients in the United States (LEAP-US) | Abnormalities, Multiple, Alagille syndrome, Cardiovascular Abnormalities, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, bile duct disorder, biliary tract disorder, cardiovascular disorder, cholestasis, congenital heart disease, hereditary disease, intrahepatic cholestasis, liver disorder, progressive familial intrahepatic cholestasis type 1 | Recruiting | Not stated | 2026-10-08 | NCT06193928 | |
| A Study of the Effectiveness, Safety and the Long-term Outcomes of Participants With Progressive Familial Intrahepatic Cholestasis (PFIC) Who Take Odevixibat (Bylvay) in China | progressive familial intrahepatic cholestasis type 1 | Recruiting | Not stated | 2026-10-01 | NCT07588880 | |
| Odevixibat Outcomes in Patients With PFIC Versus an External Control Cohort (OvEC-PFIC) | progressive familial intrahepatic cholestasis type 1 | Active, not recruiting | Not stated | 2026-10-01 | NCT07497724 | |
| A Study of the Effectiveness, Safety and the Long-term Outcomes of Participants With Progressive Familial Intrahepatic Cholestasis (PFIC) Who Take Odevixibat (Bylvay) in South Korea | progressive familial intrahepatic cholestasis type 1 | Recruiting | Not stated | 2026-10-01 | NCT07185919 | |
| Long-Term Low-Intervention SafEty and Clinical Outcomes Clinical Study of LivmArli® in Patients With Alagille Syndrome or Progressive Familial Intrahepatic Cholestasis in the European Union (LEAP-EU) | Abnormalities, Multiple, Alagille syndrome, Cardiovascular Abnormalities, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, Pathological Conditions, Signs and Symptoms, Pruritus, Signs and Symptoms, Skin Manifestations, Skin and Connective Tissue Diseases, bile duct disorder, biliary tract disorder, cardiovascular disorder, cholestasis, congenital heart disease, hereditary disease, intrahepatic cholestasis, liver disorder, progressive familial intrahepatic cholestasis type 1, skin disorder | Recruiting | Phase 4 | 2026-06-23 | NCT07290257 | |
| Dental Dyschromia and Quality of Life in Early Prolonged Hyperbilirubinemia | Abnormalities, Multiple, Alagille syndrome, Cardiovascular Abnormalities, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Dental Diseases, Digestive System Abnormalities, Digestive System Diseases, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Stomatognathic Diseases, Tooth Discoloration, bile duct disorder, biliary atresia, biliary tract disorder, cardiovascular disorder, cholestasis, congenital heart disease, hereditary disease, hyperbilirubinemia, intrahepatic cholestasis, liver disorder, progressive familial intrahepatic cholestasis type 1, tooth disorder | Recruiting | Not stated | 2026-05-12 | NCT06506734 | |
| DEFINING THE GENETIC DRIVERS OF ADULT-ONSET CHOLESTATIC LIVER DISEASE | progressive familial intrahepatic cholestasis type 1 | Recruiting | Not applicable | 2026-03-27 | NCT07317193 | |
| A Database Study of Maralixibat (TAK-625) in Participants With Alagille Syndrome (ALGS) and Progressive Familial Intrahepatic Cholestasis (PFIC) | Abnormalities, Multiple, Alagille syndrome, Cardiovascular Abnormalities, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, bile duct disorder, biliary tract disorder, cardiovascular disorder, cholestasis, congenital heart disease, hereditary disease, intrahepatic cholestasis, liver disorder, progressive familial intrahepatic cholestasis type 1 | Recruiting | Not stated | 2026-02-20 | NCT07293897 | |
| Prospective Analysis of the Treatment of Progressive Familial Intrahepatic Cholestasis (TreatFIC) | progressive familial intrahepatic cholestasis type 1 | Recruiting | Not stated | 2025-01-24 | NCT06778174 | |
| Genotype-phenotype Relationship Between Cryptogenic Cholestasis and Familial Intrahepatic Cholestasis | Digestive System Diseases, bile duct disorder, biliary tract disorder, cholestasis, intrahepatic cholestasis, liver disorder, progressive familial intrahepatic cholestasis type 1 | Recruiting | Not stated | 2025-01-17 | NCT06781242 | |
| NAtural Course and Prognosis of PFIC and Effect of Biliary Diversion | progressive familial intrahepatic cholestasis type 1 | Enrolling by invitation | Not stated | 2025-01-17 | NCT03930810 | |
| Familial Intrahepatic Cholestasis-related Genes Associated with Disease Susceptibility in Hepato-biliary Cancers | progressive familial intrahepatic cholestasis type 1 | Recruiting | Not stated | 2025-01-16 | NCT06777914 |