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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Long-Term Follow-up of Subjects With Fanconi Anaemia Subtype A Treated With ex Vivo Gene TherapyBone Marrow Failure Disorders, Congenital Bone Marrow Failure Syndromes, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, DNA repair disease, Fanconi anemia, Fanconi anemia complementation group A, Fanconi renotubular syndrome, Female Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Hemic and Lymphatic Diseases, Male Urogenital Diseases, Nutritional and Metabolic Diseases, Urogenital Diseases, anemia, aplastic anemia, bone marrow disorder, hematologic disorder, hereditary disease, inherited aplastic anemia, kidney disorder, metabolic disease, renal tubular transport disease, urinary system disorderActive, not recruitingNot stated2026-04-13NCT04437771
Gene Therapy for Fanconi Anemia, Complementation Group ABone Marrow Failure Disorders, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Fanconi anemia complementation group A, Fanconi renotubular syndrome, Female Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Hemic and Lymphatic Diseases, Male Urogenital Diseases, Urogenital Diseases, anemia, bone marrow disorder, hematologic disorder, hereditary disease, kidney disorder, renal tubular transport disease, urinary system disorderActive, not recruitingPhase 22025-12-22NCT04248439