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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Gene Therapy for Fanconi Anemia, Complementation Group ABone Marrow Failure Disorders, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Fanconi anemia complementation group A, Fanconi renotubular syndrome, Female Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Hemic and Lymphatic Diseases, Male Urogenital Diseases, Urogenital Diseases, anemia, bone marrow disorder, hematologic disorder, hereditary disease, kidney disorder, renal tubular transport disease, urinary system disorderActive, not recruitingPhase 22025-12-22NCT04248439

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OrganizationsLinked trials
Rocket Pharmaceuticals Inc.10

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Research sitesCityCountryLinked trials
Stanford UniversityStanfordUnited States24
University of MinnesotaMinneapolisUnited States30